Cancer and Blood Diseases Institute

Publications

Abu-Shihab, Y; Nicolet, D; Mrózek, K; Routbort, M; Patel, KP; Walker, CJ; Buss, J; Stiff, A; Laganson, A; DiNardo, CD; et al. BRAF-Mutated Acute Myeloid Leukemia (AML) Represents a Distinct, Prognostically Poor Subgroup Enriched in Myelodysplasia-Related (MR-)AML. Blood. 2023; 142:1575.

Adair, JE; Androski, L; Bayigga, L; Bazira, D; Brandon, E; Dee, L; Deeks, S; Draz, M; Dubé, K; Dybul, M; et al. Towards access for all: 1st Working Group Report for the Global Gene Therapy Initiative (GGTI). Gene Therapy (Basingstoke). 2023; 30:216-221.

Alharbi, H; Daniel, EJ P; Thies, J; Chang, I; Goldner, DL; Ng, BG; Witters, P; Aqul, A; Velez-Bartolomei, F; Enns, GM; et al. Fractionated plasma N-glycan profiling of novel cohort of ATP6AP1-CDG subjects identifies phenotypic association. Journal of Inherited Metabolic Disease. 2023; 46:300-312.

Ambrose, EE; Latham, TS; Songoro, P; Charles, M; Lane, AC; Stuber, SE; Makubi, AN; Ware, RE; Smart, LR. Hydroxyurea with dose escalation for primary stroke risk reduction in children with sickle cell anaemia in Tanzania (SPHERE): an open-label, phase 2 trial. The Lancet Haematology. 2023; 10:e261-e271.

Anand, M; Nysather, J; McGraw, G; Apewokin, S; Khoury, R; Grimley, MS; Bumb, S; Govil, A. Viral specific T cell therapy in kidney transplant recipients - A single-center experience. Transplant Infectious Disease. 2023; 25:e14179.

Arnold, DE; Kaviany, S; Aluri, J; Murguia-Favela, L; Wright, NA; Loughran, TP; Powell, J; De Ravin, SS; Rao, VK; Holland, S; et al. Clinical Characteristics, Management, and Allogeneic Hematopoietic Cell Transplantation of Patients with Toll-like Receptor 8 Gain-of-Function Mutations. Blood. 2023; 142:936.

Auletta, JJ; Holter-Chakrabarty, J; Jain, T; Miller, B; Ward, E; Khera, N; Gomez-Arteaga, A; Hall, A; Nemecek, E; Robb, D; et al. Proceedings of the 2023 Second Annual ASTCT-NMDP ACCESS Initiative Workshop. Transplantation and cellular therapy. 2023; 29:739-746.

Auletta, JJ; Khera, N; DeMartino, P; Kelkar, AH; Yusuf, RA; Davies, SM; Knutson, J; Beaver, E; Maloney, A; Majhail, NS. Assessing Medicaid Coverage for Hematopoietic Cell Transplantation and Chimeric Antigen Receptor T Cell Therapy: A Project from the American Society for Transplantation and Cellular Therapy and the National Marrow Donor Program ACCESS Initiative. Transplantation and cellular therapy. 2023; 29:713-720.

Azhar, M; Kincaid, Z; Kesarwani, M; Menke, J; Schwieterman, J; Ansari, S; Reaves, A; Ahmed, A; Shehzad, R; Khan, A; et al. Rational polypharmacological targeting of FLT3, JAK2, ABL, and ERK1 suppresses the adaptive resistance to FLT3 inhibitors in AML. Blood Advances. 2023; 7:1460-1476.

Azucenas, CR; Stewart, M; Voulgaridou, A; Seu, K; Kalfa, TA. Inducible Knockout of Codanin-1: An Adult Mouse Model of Congenital Dyserythropoietic Anemia Type-I. Blood. 2023; 142:2450.

Babic, I; Bryan, N; Cunningham, C; Sampson, A; Starczynowski, D; Nurmemmedov, E. Abstract 2759: Real-time cellular target engagement and protein quantification for drug discovery. Cancer Research. 2023; 83:2759.

Bahakel, H; Spieker, AJ; Stahl, A; Rahman, H; Amarin, J; Hamdan, L; Dulek, DE; Kitko, CL; Batarseh, E; Haddadin, Z; et al. Immunogenicity and Safety of Alternative Influenza Vaccination Strategies in Repeated Seasons in Pediatric Hematopoietic-Cell Transplant Recipients. Journal of the Pediatric Infectious Diseases Society. 2023; 12:s21.

Bareja, R; Ismail, M; Martin, D; Nayate, A; Yadav, I; Labbad, M; Tamrazi, B; Salloum, R; Margol, A; Judkins, A; et al. MDB-44. A TRANSFER LEARNING APPROACH FOR AUTOMATIC SEGMENTATION OF TUMOR SUB-COMPARTMENTS AND TUMOR HABITAT IN PEDIATRIC MEDULLOBLASTOMA. Neuro-Oncology. 2023; 25:i71-i72.

Bareja, R; Ismail, M; Martin, D; Nayate, A; Yadav, I; Labbad, M; Tamrazi, B; Salloum, R; Margol, A; Judkins, A; et al. MDB-43. GRADIENT ENTROPY-BASED RADIOMIC RISK-SCORE FROM T1-WEIGHTED PRE-TREATMENT MRI SCANS CAN PREDICT SURVIVAL IN PEDIATRIC MEDULLOBLASTOMA. Neuro-Oncology. 2023; 25:i71.

Barron, T; Yalçin, B; Mochizuki, A; Cantor, E; Shamardani, K; Tlais, D; Franson, A; Lyons, S; Mehta, V; Jahan, SM; et al. CNSC-01. GABAERGIC NEURON-TO-GLIOMA SYNAPSES IN DIFFUSE MIDLINE GLIOMAS. Neuro-Oncology. 2023; 25:i11.

Bartlett, AL; Zhang, G; Wallace, G; McLean, S; Myers, KC; Teusink-Cross, A; Taggart, C; Patel, B; Davidson, R; Davies, SM; et al. Optimized vitamin D repletion with oral thin film cholecalciferol in patients undergoing stem cell transplant. Blood Advances. 2023; 7:4555-4562.

Bedard, MC; Chihanga, T; Carlile, A; Jackson, R; Brusadelli, MG; Lee, D; VonHandorf, A; Rochman, M; Dexheimer, PJ; Chalmers, J; et al. Single cell transcriptomic analysis of HPV16-infected epithelium identifies a keratinocyte subpopulation implicated in cancer. Nature Communications. 2023; 14:1975.

Bender, J; Damodharan, S; Moskop, A; Toner, K; Vatsayan, A; Capitini, C; Baggott, C; Schiff, DE; Katsanis, E; Raikar, SS; et al. Real-world use of tisagenlecleucel in children and young adults with relapsed or refractory B-cell lymphomas. Journal of Clinical Oncology. 2023; 41:10031.

Bender, JD; Oquendo-del Toro, H; Benoit, J; Howell, JC; Badia, P; Davies, SM; Grimley, MS; Jodele, S; Phillips, C; Burns, K; et al. Reduced-Intensity Conditioning Mitigates Risk for Primary Ovarian Insufficiency but Does Not Decrease Risk for Infertility in Pediatric and Young Adult Survivors of Hematopoietic Stem Cell Transplantation. Transplantation and cellular therapy. 2023; 29:130.e1-130.e8.

Bender, JD; Rubinstein, JD; Mizukawa, B; Perentesis, JP; Pommert, L. Use of gemcitabine, oxaliplatin, and anti-CD20 therapy in children and adolescents with non-Hodgkin lymphoma unfit for intensive therapy. Pediatric Blood and Cancer. 2023; 70:e30214.

Bennett, J; Ishikawa, C; Agarwal, P; Yeung, J; Sampson, A; Uible, E; Vick, E; Bolanos, LC; Hueneman, K; Wunderlich, M; et al. Paralog-specific signaling by IRAK1/4 maintains MyD88-independent functions in MDS/AML. Blood. 2023; 142:989-1007.

Betensky, M; Mosha, M; Tarango, C; Anupam, V; Bhat, R; Kucine, N; Nakano, T; Woods, G; Nakar, C; Amankwah, E; et al. OC 38.4 Transient Antiphospholipid Antibodies, Antiphospholipid Syndrome and Clinical Outcomes in Patients <21 Years Old with Provoked Venous Thromboembolism: Analysis from the Kids-DOTT Multinational Trial. Research and Practice in Thrombosis and Haemostasis. 2023; 7:100519.

Bilston, L; Uminski, K; Kalfa, TA; Husami, A; Goodyear, MD; Rydz, N. A Novel Beta Globin Frameshift Mutation Causing Autosomal Dominant Beta Thalassemia. Blood. 2023; 142:1105.

Borst, AJ; Hammill, AM; Crary, SE; McLean, TW; Felton, T; Blatt, J. Barriers to Genetic Testing in Vascular Malformations. JAMA Network Open. 2023; 6:e2314829.

Bouffi, C; Wikenheiser-Brokamp, KA; Chaturvedi, P; Sundaram, N; Goddard, GR; Wunderlich, M; Brown, NE; Staab, JF; Latanich, R; Zachos, NC; et al. In vivo development of immune tissue in human intestinal organoids transplanted into humanized mice. Nature Biotechnology. 2023; 41:824-831.

Brivio, E; Pennesi, E; Willemse, M; Jiang, Y; van der Velden, V; Beverloo, B; Hudson, C; Kuttschreuter, L; van der Sluis, I; Brethon, B; et al. P676: UPDATED RESULTS FROM THE TRIAL ITCC-054/COG-AAML1921: BOSUTINIB IN NEWLY DIAGNOSED AND RESISTANT/INTOLERANT PEDIATRIC PATIENTS WITH CHRONIC MYELOID LEUKEMIA. HemaSphere. 2023; 7:e506783a.

Broder, MS; Adams, DM; Canaud, G; Collins, C; Davis, K; Frieden, IJ; Gibbs, SN; Hammill, AM; Keppler-Noreuil, KM; Nakano, TA; et al. RAND/UCLA Modified Delphi Panel on the Severity, Testing, and Medical Management of PIK3CA-Related Spectrum Disorders (PROS). 2023; 4:e067.

Burke, GA A; Vinti, L; Kabickova, E; Beishuizen, A; Tacyildiz, N; Uyttebroeck, A; Kang, HJ; Luisi, F; Minard-Colin, V; Burkhardt, B; et al. Ibrutinib plus RICE or RVICI for relapsed/refractory mature B-cell non-Hodgkin lymphoma in children and young adults: SPARKLE trial. Blood Advances. 2023; 7:602-610.

Butler-Foster, T; Khandelwal, A; Montemayor, C; Miller, YM; Yan, MT S; Holmberg, JA; Ipe, TS; Accooe, P; Cancelas, JA. From MPOX to the next epidemic: Words matter when talking about equity-deserving groups. Transfusion. 2023; 63:646-651.

Cantrell, R; Feldman, H; Rosenfeldt, L; Ali, A; Sharma, B; Revenko, A; Monia, B; Waggoner, S; Palumbo, J. PB0727 The Role of Thrombin and Thrombin Signaling in Chronic LCMV Infection. Research and Practice in Thrombosis and Haemostasis. 2023; 7:101315.

Ceolan, J; Seu, K; Ntoumaziou, A; Elgammal, Y; Emberesh, S; Bilston, L; Richards, D; Dickerson, KE; Chonat, S; Rydz, N; et al. Erythrocyte Disorders Mimicking Congenital Dyserythropoietic Anemia Based on Bone Marrow Pathology Exposed By Genetic Evaluation. Blood. 2023; 142:2459.

Chandrasekaran, P; Han, Y; Zerbe, CS; Heller, T; DeRavin, SS; Kreuzberg, SA; Marciano, BE; Siu, Y; Jones, DR; Abraham, RS; et al. Intestinal microbiome and metabolome signatures in patients with chronic granulomatous disease. Journal of Allergy and Clinical Immunology. 2023; 152:1619-1633.e11.

Chlon, TM; Patnaik, MM. Germline DDX41 mutant predisposition syndromes: Slow driver states to hematological malignancies. American Journal of Hematology. 2023; 98:1673-1676.

Chlon, TM; Stepanchick, E; Sulentic, A; Wilson, A; Starczynowski, DT. Abstract A46: Heterozygous mutations in DDX41 cause erythroid progenitor cell defects and cooperate with p53 mutations to cause hematologic malignancy. 2023; 4:a46.

Cohen, C; Powers, J; Tarango, C. Emicizumab Use in Infancy: A Survey of United States Pediatric Hemophilia Treatment Center Medical Directors. Blood. 2023; 142:1242.

Cohen-Cutler, S; Blatt, J; Bayliff, S; Iacobas, I; Hammill, A; Sisk, BA. Vascular Anomalies Care in the United States: A Cross-Sectional National Survey. The Journal of Pediatrics. 2023; 261:113579.

Coleman, KD; McKinley, K; Ellison, AM; Alpern, ER; Hariharan, S; Topoz, I; Wurtz, M; Nielsen, B; Cook, LJ; Morris, CR; et al. Return visit rates after an emergency department discharge for children with sickle cell pain episodes. Pediatric Blood and Cancer. 2023; 70:e30553.

Coleman, KD; McKinley, K; Ellison, AM; Alpern, ER; Hariharan, S; Topoz, I; Wurtz, M; Nielsen, B; Cook, LJ; Morris, CR; et al. Association between Acute Pain Scores in Children with Sickle Cell Disease and Emergency Department Disposition and Return Visit Rates. Blood. 2023; 142:3874.

Cooke-Barber, J; Brungardt, JG; Sorger, M; Pressey, JG; Turpin, B; Nagarajan, R; Szabo, S; Sorger, J; Johnson, N; Dasgupta, R. ASO Author Reflections: Minimizing Time in Hospital via Bone Biopsy or Other Means. Annals of Surgical Oncology. 2023; 30:3666.

Cooke-Barber, J; Brungardt, JG; Sorger, M; Pressey, JG; Turpin, B; Nagarajan, R; Szabo, S; Sorger, J; Johnson, N; Dasgupta, R. ASO Visual Abstract: Pediatric and Young Adult Image-Guided Percutaneous Bone Biopsy-A New Standard of Care?. Annals of Surgical Oncology. 2023; 30:3667.

Cooke-Barber, J; Brungardt, JG; Sorger, M; Pressey, JG; Turpin, B; Nagarajan, R; Szabo, S; Sorger, J; Johnson, N; Dasgupta, R. Pediatric and Young Adult Image-Guided Percutaneous Bone Biopsy-A New Standard of Care?. Annals of Surgical Oncology. 2023; 30:3658-3665.

Coppola, T; Perrone, O; Batram, J; Nasr, W; Treichel, S; Xu, J; Myers, K; Filippi, M. Human Hematopoietic Stem Cells Have Altered Mitochondrial Activity after Stem Cell Transplantation. Blood. 2023; 142:3430.

Crosby, LE; Lang, A; Mara, C; Quinn, CT; Schultz, CL; Bear, B; Akintobi, TE; Miller, RE; Hildenbrand, AK. Patterns of Nonadherence to Hydroxyurea in Pediatric Sickle Cell Disease. Blood. 2023; 142:7198.

Cullion, K; Ostertag-Hill, CA; Pan, M; Timko, B; Boscolo, E; Kohane, DS. Ablation of Venous Malformations by Photothermal Therapy with Intravenous Gold Nanoshells. Nano Letters: a journal dedicated to nanoscience and nanotechnology. 2023; 23:7092-7099.

D’Alessandro, PR. Research-Based Theater in the Pediatric Oncology Setting: Balancing Ethical Tensions. Qualitative Inquiry. 2023; 29:305-313.

Dandamudi, A; Akbar, H; Cancelas, J; Zheng, Y. Rho GTPase Signaling in Platelet Regulation and Implication for Antiplatelet Therapies. International Journal of Molecular Sciences. 2023; 24:2519.

Dandamudi, A; Seibel, W; Tourdot, B; Cancelas, JA; Akbar, H; Zheng, Y. Structure-Activity Relationship Analysis of Rhosin, a RhoA GTPase Inhibitor, Reveals a New Class of Antiplatelet Agents. International Journal of Molecular Sciences. 2023; 24:4167.

Dandoy, CE; Tsong, WH; Sarikonda, K; McGarvey, N; Perales, MA. Systematic Review of Signs and Symptoms Associated with Hematopoietic Stem Cell Transplantation-Associated Thrombotic Microangiopathy. Transplantation and cellular therapy. 2023; 29:282.e1-282.e9.

Daugherty, EC; Mascia, A; Zhang, Y; Lee, E; Xiao, Z; Sertorio, M; Woo, J; McCann, C; Russell, K; Levine, L; et al. FLASH Radiotherapy for the Treatment of Symptomatic Bone Metastases (FAST-01): Protocol for the First Prospective Feasibility Study. JMIR Research Protocols. 2023; 12:e41812.

de Blank, P; Nishiyama, A; López-Juárez, A. A new era for myelin research in Neurofibromatosis type 1. Glia. 2023; 71:2701-2719.

Dean, ST; Ishikawa, C; Zhu, X; Walulik, S; Nixon, T; Jordan, JK; Henderson, S; Wyder, M; Salomonis, N; Wunderlich, M; et al. Repression of TRIM13 by chromatin assembly factor CHAF1B is critical for AML development. Blood Advances. 2023; 7:4822-4837.

Deng, L; Costa, F; Blake, KJ; Choi, S; Chandrabalan, A; Yousuf, MS; Shiers, S; Dubreuil, D; Vega-Mendoza, D; Rolland, C; et al. S. aureus drives itch and scratch-induced skin damage through a V8 protease-PAR1 axis. Cell. 2023; 186:5375-5393.e25.

Doherty, AC; Huddleston, DA; Horn, PS; Ratner, N; Simpson, BN; Schorry, EK; Aschbacher-Smith, L; Prada, CE; Gilbert, DL. Motor Function and Physiology in Youth With Neurofibromatosis Type 1. Pediatric Neurology. 2023; 143:34-43.

Dong, M; Ware, RE; Dallmann, A; Vinks, AA. Hydroxyurea treatment for sickle cell anemia during pregnancy and lactation: Current evidence and knowledge gaps. Pharmacotherapy: The Journal of Human Pharmacology and Drug Therapy. 2023; 43:419-429.

Dourson, AJ; Fadaka, AO; Warshak, AM; Paranjpe, A; Weinhaus, B; Queme, LF; Hofmann, MC; Evans, HM; Donmez, OA; Forney, C; et al. Macrophage epigenetic memories of early life injury drive neonatal nociceptive priming. 2023; 4:2023.02.13.528015.

Dunseath, C; O'Connor, G; Mahulkar, S; Badia, P; Koo, J; Dandoy, CE. Incidence of Bloodstream Infections after Hematopoietic Stem Cell Transplantation for Hurler Syndrome. Transplantation and cellular therapy. 2023; 29:707.e1-707.e4.

Dvorak, CC; Haddad, E; Heimall, J; Dunn, E; Cowan, MJ; Pai, SY; Kapoor, N; Satter, LF; Buckley, RH; O'Reilly, RJ; et al. The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions. Journal of Allergy and Clinical Immunology. 2023; 151:547-555.e5.

Earley, EJ; Kelly, S; Fang, F; Alencar, CS; Rodrigues, DD O W; Soares Cruz, DT; Flanagan, J; Ware, RE; Zhang, X; Gordeuk, V; et al. Genome-wide association study of early ischaemic stroke risk in Brazilian individuals with sickle cell disease implicates ADAMTS2 and CDK18 and uncovers novel loci. British Journal of Haematology. 2023; 201:343-352.

Eldem, I; Picarsic, J; Kumar, A; Mossé, YP; Roberts, KF; Armstrong, AE; Sisk, BA. Lorlatinib use in an infant with thalamic ALK-positive histiocytosis. Pediatric Blood and Cancer. 2023; 70:e30378.

Elgammal, Y; Risinger, M; Husami, A; Walden, J; Gupta, S; Shah, NC; Boyer, J; Abajas, YL; Winstead, M; Miller, DW; et al. Congenital Dyserythropoietic Anemia Type II: An Update from the Congenital Dyseryhtropoietic Anemia Registry of North America (CDAR). Blood. 2023; 142:1079.

Engel, ER; Hammill, A; Adams, D; Phillips, RJ; Jeng, M; Tollefson, MM; Iacobas, I; Schiff, D; Greenberger, S; Kelly, M; et al. Response to sirolimus in capillary lymphatic venous malformations and associated syndromes: Impact on symptomatology, quality of life, and radiographic response. Pediatric Blood and Cancer. 2023; 70:e30215.

Fan, C; Wunderlich, M; Cai, X; Yan, Z; Zhang, F; Davis, AK; Xu, L; Guo, F; Lu, QR; Azam, M; et al. Kinase-independent role of mTOR and on-/off-target effects of an mTOR kinase inhibitor. Leukemia. 2023; 37:2073-2081.

Fenchel, L; Jackson, F; Walker, B; Manuel, C; Hooks, D; Allen, T; Thant, MM; Karkoska, K; Smart, LR; Joffe, NE; et al. Improving Transition of Emerging Adults with Sickle Cell Disease to Adult Care through a Multidisciplinary Process: The Development of a Transition Clinic to Support Transition Success. Blood. 2023; 142:5055.

Fichter, KM; Setayesh, T; Malik, P. Strategies for precise gene edits in mammalian cells. Molecular Therapy-Nucleic Acids. 2023; 32:536-552.

Filippi, MD. The multifaceted role of mitochondria in HSC fate decisions: energy and beyond. Experimental Hematology. 2023; 128:19-29.

Forlenza, CJ; Rosenzweig, J; Mauguen, A; Buhtoiarov, I; Cuglievan, B; Dave, H; Deyell, RJ; Flerlage, JE; Franklin, AK; Krajewski, J; et al. Brentuximab vedotin after autologous transplantation in pediatric patients with relapsed/refractory Hodgkin lymphoma. Blood Advances. 2023; 7:3225-3231.

Galletta, TJ; Dong, M; Vinks, AA; Chiang, SC C; Teusink-Cross, A; Marsh, RA; Davies, SM; Mehta, PA; Khandelwal, P. 356 Children Under 2 Years Old Treated with Ruxolitinib for Acute and Chronic Graft-Versus-Host-Disease Demonstrate Variable Pharmacokinetics. Transplantation and cellular therapy. 2023; 29:s271-s272.

Galletta, TJ; Lane, A; Lutzko, C; Leemhuis, T; Cancelas, JA; Khoury, R; Wang, YZ M; Hanley, PJ; Keller, MD; Bollard, CM; et al. Third-Party and Patient-Specific Donor-Derived Virus-Specific T Cells Demonstrate Similar Efficacy and Safety for Management of Viral Infections after Hematopoietic Stem Cell Transplantation in Children and Young Adults. Transplantation and cellular therapy. 2023; 29:305-310.

Galletta, TJ; Rubinstein, JD; Krupski, C; Nelson, AS; Khoury, R; Dandoy, CE; Davies, SM; Phillips, CL. Durable remissions achieved with reinfusion of CD19-directed CAR-T despite failure to induce or maintain B-cell aplasia and single-center experience with reinfusion of tisagenlecleucel. Pediatric Blood and Cancer. 2023; 70:e30271.

Garland, K; Mullins, E; Bercovitz, RS; Rodriguez, V; Connors, J; Sokkary, N. Hemostatic considerations for gender affirming care. Thrombosis Research. 2023; 230:126-132.

Garrett, MC; Albano, R; Carnwath, T; Elahi, L; Behrmann, CA; Pemberton, M; Woo, D; O’Brien, E; VanCauwenbergh, B; Perentesis, J; et al. HDAC1 and HDAC6 are essential for driving growth in IDH1 mutant glioma. Scientific Reports. 2023; 13:12433.

Geerlinks, AV; Scull, B; Krupski, C; Fleischmann, R; Pulsipher, MA; Eapen, M; Connelly, JA; Bollard, CM; Pai, S; Duncan, CN; et al. Alemtuzumab and CXCL9 levels predict likelihood of sustained engraftment after reduced-intensity conditioning HCT. Blood Advances. 2023; 7:3725-3734.

Gonzalez, LS; Fisher, AA; D'souza, SP; Cotella, EM; Lang, RA; Robinson, JE. Ventral striatum dopamine release encodes unique properties of visual stimuli in mice. eLife. 2023; 12:e85064.

Gonzalez-Muñoz, T; Giannatale, AD; García-Silva, S; Santos, V; Sanchez-Redondo, S; Savini, C; Graña-Castro, O; Blanco-Aparicio, C; Fischer, S; De Wever, O; et al. Endoglin, a Novel Biomarker and Therapeutical Target to Prevent Malignant Peripheral Nerve Sheath Tumor Growth and Metastasis. Clinical Cancer Research. 2023; 29:3744-3758.

Gorak, EJ; Otterstatter, M; Al Baghdadi, T; Gillis, N; Foran, JM; Liu, JJ; Bejar, R; Gore, SD; Kroft, SH; Harrington, A; et al. Discordant pathologic diagnoses of myelodysplastic neoplasms and their implications for registries and therapies. Blood Advances. 2023; 7:6120-6129.

Gossai, N; Bhojwani, D; Schafer, ES; Chang, BH; Pommert, L; Verma, A; Malvar, J; Chi, YY; Hitzler, J; Burke, MJ; et al. Patients with Down syndrome can be included in early phase clinical trials- a report from the T2016-003 Therapeutic Advances in Childhood Leukemia and Lymphoma (TACL) study. Leukemia. 2023; 37:1138-1140.

Gounder, M; Ratan, R; Alcindor, T; Schöffski, P; Van Der Graaf, WT; Wilky, BA; Riedel, RF; Lim, A; Smith, LM; Moody, S; et al. Nirogacestat, a γ-Secretase Inhibitor for Desmoid Tumors. The New England journal of medicine. 2023; 388:898-912.

Grimley, M; Maron, G; Gomez, CA; Prasad, VK; Dara, J; Papanicolaou, GA; Fukushima, K; Wynn, RF; Boeckh, M. Preliminary Results of a Phase 2a Clinical Trial to Evaluate Safety, Tolerability and Antiviral Activity of Intravenous Brincidofovir (BCV IV) in Immunocompromised Patients with Adenovirus Infection. Blood. 2023; 142:112.

Grover, SP; Bharathi, V; Posma, JJ; Griffin, JH; Palumbo, JS; Mackman, N; Antoniak, S. Thrombin-mediated activation of PAR1 enhances doxorubicin-induced cardiac injury in mice. Blood Advances. 2023; 7:1945-1953.

Gurska, LM; Okabe, R; Schurer, A; Tong, MM; Soto, M; Choi, D; Ames, K; Glushakow-Smith, S; Montoya, A; Tein, E; et al. Crizotinib Has Preclinical Efficacy in Philadelphia-Negative Myeloproliferative Neoplasms. Clinical Cancer Research. 2023; 29:943-956.

Guzman-Gomez, A; Ahmed, HF; Dani, A; Zafar, F; Lehenbauer, DG; Potter, AS; Morales, DL S; Ziady, AG; Hayes, D. Center volume effect on acute cellular rejection and outcomes in pediatric lung transplant recipients. Journal of Heart and Lung Transplantation. 2023; 42:1030-1039.

Guzman-Gomez, A; Skala, E; Dani, A; Sharma, N; Ziady, A; Hayes, D. Sex and Sex Hormones Matter in Lung Transplant Outcomes. Journal of Heart and Lung Transplantation. 2023; 42:s141.

Han, L; Dong, L; Leung, K; Zhao, Z; Li, Y; Gao, L; Chen, Z; Xue, J; Qing, Y; Li, W; et al. METTL16 drives leukemogenesis and leukemia stem cell self-renewal by reprogramming BCAA metabolism. Cell Stem Cell. 2023; 30:52-68.e13.

Hashimoto, M; Li, J; Andreassen, PR; Huang, G. CPT1a Controls the Function of Long-Term Hematopoietic Stem Cells By Regulating the Balance between Fatty Acid Oxidation and Oxphos in Mitochondria. Blood. 2023; 142:4089.

Hayes, D; Dani, A; Guzman-Gomez, A; Zafar, F; Morales, DL S; Ziady, AG. Changing racial and ethnic differences for lung transplantation in cystic fibrosis. Pediatric Transplantation. 2023; 27:e14404.

Heczey, A; Xu, X; Courtney, AN; Tian, G; Barragan, GA; Guo, L; Amador, CM; Ghatwai, N; Rathi, P; Wood, MS; et al. Anti-GD2 CAR-NKT cells in relapsed or refractory neuroblastoma: updated phase 1 trial interim results. Nature Medicine. 2023; 29:1379-1388.

Hegde, S; Nestheide, S; Wellndorf, A; Zheng, Y; Cancelas, J. 3080 – RHOA SIGNALING IS REQUIRED FOR THE COLD-INDUCED PLATELET LESION AND REVERSIBLE TARGETING OF RHOA IN A NEW PLATELET ADDITIVE SOLUTION EXTENDS DONOR-DERIVED PLATELET SHELF-LIFE TO FOURTEEN DAYS. Experimental Hematology. 2023; 124:s90.

Hennigan, RF; Thomson, CS; Stachowski, K; Nassar, N; Ratner, N. Merlin tumor suppressor function is regulated by PIP2-mediated dimerization. Editor, van der Wel P. PloS one. 2023; 18:e0281876.

Hernández, G; Romero-Cortadellas, L; Ferrer-Cortès, X; Venturi, V; Dessy-Rodriguez, M; Olivella, M; Husami, A; de Soto, CP; Morales-Camacho, RM; Villegas, A; et al. Mutations in the RACGAP1 gene cause autosomal recessive congenital dyserythropoietic anemia type III. Haematologica: the hematology journal. 2023; 108:581-587.

Hildenbrand, AK; Kidwell, KM; McGrady, ME; Quinn, CT; Crosby, LE; Mara, CA. Feasibility of Electronic Medication Monitoring Among Adolescents and Emerging Adults with Sickle Cell Disease. Patient Preference and Adherence. 2023; 17:3167-3171.

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Ratner, N; Hu, L; Pundavela, J; Epstein, JA. Abstract IA17: Use of RAS isoforms in nerve tumors. Molecular cancer research : MCR. 2023; 21:ia17.

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