Who can participate?
Adults who have a diagnosis of aPAP may be eligible to be in this study.
What will happen in the study?
This study will last up to 108 weeks (about 2 years). It will require 17 visits to the clinic site.
Here are some of the things that will happen in this study:
- Be asked to perform screening tests and procedures to figure out if you qualify for the study. You will visit the clinic site 2 times (visit 1-2). You will not receive any treatment.
- Receive either the study drug or placebo every day for 48 weeks. You will visit the clinic site 9 times.
- If you complete the first 48 week, you may choose to receive study drug every day for another 48 weeks. You will visit the clinic site 4 times and have one phone call with the study team.
- A safety follow-up visit will occur 4 weeks later to ensure there has not been development of any late side effects.
What are the good things that can happen from this research?
There is a possibility that you will benefit from an improvement in your aPAP symptoms when you receive the study drug for at least 48 weeks.
Will you/your child be paid to be in this research study?
If you complete this study, we may pay you up to $1,275.00.