Bone Marrow Transplantation and Immune Deficiency

Publications

Abdullah, S; Sabulski, A; Hudda, Z; Ziady, A; Luebbering, N; Giordullo, L; Odegard, E; Blackard, JT; Kleiboeker, S; Altrich, M; Jodele, S; Seif, AE; Davies, SM; Laskin, BL. Susceptibility to BK polyomavirus-associated hemorrhagic cystitis in children undergoing allogeneic transplant. Haematologica. 2025; 110(2):527-531.

Abdullah, S; Sabulski, A; Hudda, Z; Ziady, AG; Luebbering, N; Langenberg, L; Odegard, E; Blackard, JT; Kleiboeker, S; Jodele, S; Seif, AE; Davies, SM; Laskin, B. Bkpyv Replication Kinetics and Association with Hemorrhagic Cystitis in Pediatric HSCT Recipients. Transplantation and Cellular Therapy. 2025; 31(2):s515-s516.

Abid, MB; Wudhikarn, K; Ye, Q; Martens, M; Mirza, A-S; Gowda, L; Devarakonda, S; Efebera, Y; Boghdadly, ZE; Dandoy, C; Murthy, H; Perales, M-A; Huppler, A; Auletta, J. Infections in patients with relapsed refractory multiple myeloma receiving idecabtagene vicleucel therapy: A real-world analysis from CIBMTR. Blood. 2025; 146(Supplement 1):716.

Abts, MF; Silva Carmona, MD; Baker, KS; Ballard, S; Genatossio, A; Lane, A; Robinson, PD; Allen, JL; Koo, J; Davies, SM; Goldfarb, SB. Comparisons Between Multiple Breath Washout and Standard-of-Care Spirometry in Children Undergoing Allogenic Hematopoietic Stem Cell Transplant: A Transpire Study. American Journal of Respiratory and Critical Care Medicine. 2025; 211(Supplement_1):a5125-a5125.

Alexander, JL; Dávila Saldaña, BJ; Brazauskas, R; Dammalapati, SG; Griffith, LM; Shah, AJ; Shimano, KA; Ochs, HD; Bleesing, J; Ebens, CL; Cowan, MJ; Petrovic, A; Pai, S-Y; Burroughs, LM. Hematopoietic Cell Transplantation for Wiskott-Aldrich syndrome: A PIDTC Report. Blood advances. 2025.

Alexander, JL; Saldana, BJD; Brazauskas, R; Dammalapati, SG; Griffith, LM; Shah, AJ; Shimano, KA; Ochs, HD; Bleesing, JJ; Ebens, CL; Petrovic, A; Pai, S-Y; Burroughs, LM; Chan, A. Hematopoietic Cell Transplantation for Wiskott-Aldrich Syndrome - Impact of Age, Donor, and Infection: A Pidtc Report. Transplantation and Cellular Therapy. 2025; 31(2):s39-s41.

Almodallal, Y; Whitehurst, D; Way, SS; Koo, J; Kumar, AR. Emapalumab for Maladaptive Interferon-γ-Mediated Inflammation in Drug Reaction With Eosinophilia and Systemic Symptoms Complicating First-Line Antituberculosis Therapy. Pediatric Blood and Cancer. 2025; 72(12):e32052.

Andresen, F; Myers, KC; Guttierez, A; Schwarz, D; Goldberg, B; Weller, E; Reilly, C; Brundige, K; Loveless, S; Cheng, L; Lindsley, C; Shimamura, A. CONCORDANCE OF SOMATIC GENETIC TESTING IN BLOOD VS. BONE MARROW IN SHWACHMAN-DIAMOND SYNDROME. EJC Paediatric Oncology. 2025; 6:100332.

Arnold, DE; Kaviany, S; Aluri, J; Calvo, KR; Mehta, SS; Tobin, JM; Schuettpelz, L; Saucier, N; Schmitz, EG; Murguía-Favela, L; Pai, S-Y; Bednarski, JJ; Connelly, JA; Cooper, MA. Clinical Characteristics, Management, and Hematopoietic Cell Transplantation of Patients with TLR8 Gain-of-Function. Blood advances. 2025.

Arnold, DE; Leiding, JW; Logan, B; Marsh, RA; Griffith, LM; Grunebaum, E; Murguía-Favela, L; Mallhi, K; Chellapandian, D; Deal, CL; Torgerson, T; Malech, HL; Kang, EM; Parikh, S. Umbilical Cord Blood Transplantation Provides an Alternative for Patients With Chronic Granulomatous Disease Lacking HLA-Matched Donors: A PIDTC Report. Transplantation and Cellular Therapy. 2026; 32(1):89.e1-89.e10.

Ashraf, A; Murphey, C; Sper, C; Webster, A; Lane, A; Mesa, S; Garcia, F; Perez, R; Chamblin, C; Davies, SM; Khandelwal, P. Underlying Diagnosis and RBC Transfusions Increase HLA Antibodies in Children before Hematopoietic Stem Cell Transplantation. Transplantation and Cellular Therapy. 2025.

Ashraf, A; Davies, SM; Jodele, S; Sabulski, A. A 10-Year History of Graft Failure in Pediatric Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31(2):s148-s149.

Ashraf, A; Murphey, C; Sper, C; Webster, A; Lane, A; Mesa, S; Garcia, F; Perez, R; Chamblin, C; Davies, SM; Khandelwal, P. Male Gender and Underlying Diagnosis Predisposes to Increased HLA Antibody Burden in Children before Allogeneic Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31(2):s147.

Ashraf, A; Lake, KE; Myers, KC; Towe, C; Cooper, R; Edwards, SL; Hils, B; Davies, SM; Koo, J. Frequent Pulmonary Complications after Allogeneic Hematopoietic Stem Cell Transplant: A Brief Transpire Report. Transplantation and Cellular Therapy. 2025; 31(2):s149-s150.

Bahakel, H; Spieker, AJ; Hayek, H; Schuster, JE; Hamdan, L; Dulek, DE; Kitko, CL; Stopczynski, T; Batarseh, E; Haddadin, Z; Englund, JA; Munoz, FM; Danziger-Isakov, L; Halasa, N. Immunogenicity and Reactogenicity of High- or Standard-Dose Influenza Vaccine in a Second Consecutive Influenza Season. Journal of Infectious Diseases. 2025; 231(1):e123-e131.

Bartlett, AL; Ramos, KN; Bartlett, JR; Ramos, KS; Luebbering, N; Myers, KC; Mehta, PA; Davies, SM. LINE-1 Retroelement Activation and Neuroinflammation in Persons With Fanconi Anemia. Pediatric Blood and Cancer. 2025; 72(12):e32081.

Bauchat, A; Peterson, A; Ahn, KW; Mehta, PA; Phillips, CL; Schultz, KR; Sharma, A; Broglie, L; Qayed, M. Impact of Graft Versus Host Disease Following Allogeneic Hematopoietic Cell Transplantation on Leukemia Free Survival in Hematologic Malignancies: A CIBMTR Analysis. Transplantation and Cellular Therapy. 2025; 31(2):s60-s61.

Bender, J; Davies, SM; Myers, KC; Benoit, SW. Beyond Survival: Assessing Renal and Cardiovascular Health in Fanconi Anemia Adolescents and Young Adults Post-Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31(2):s375-s376.

Bhatt, NS; Lehmann, L; Dandoy, CE; Auletta, JJ; Badia, P; Ballard, SA; Blacken, R; Daraiseh, NM; Desmond, C; Dunseath, C; Tarquini, S; Phelan, R; Pai, A; Rotz, S. Multicenter Study on Caregiver Experiences in Pediatric Hematopoietic Stem Cell Transplantation Part I: Integrative Analysis of Mental Health, Psychosocial Stressors, and Support Mechanisms. Transplantation and Cellular Therapy. 2025; 31(7):456.e1-456.e16.

Bhatt, N; Hellewell, EM; Ng, K; Gooley, TA; Taylor, AO; Hong, S; Sung, A; Ahmed, N; Morey, C; Fitzmaurice, S; Yingling, S; Edgar, C; Browning, A; Lee, CJ. Real-World Assessment of Patient Adherence to the Late Effects Screening Recommendations Among Hematopoietic Cell Transplantation Survivors. Transplantation and Cellular Therapy. 2025; 31(2):s364-s365.

Bleesing, J. The Fas-mediated apoptosis assay: From concept to clinical application. Journal of Immunological Methods. 2025; 537:113812.

Blumenstock, JA; Boge, C; Shuster, S; Li, Y; Seif, AE; Green, MD; Michaels, MG; Alexander, JL; Ardura, MI; Auletta, J; Kajon, AE; Grimley, M; Danziger-Isakov, LA; Fisher, BT. 633. Incidence and Outcomes of Pediatric Allogeneic Hematopoietic Cell Transplant (allo-HCT) Recipients Under Surveillance and Not Under Surveillance for Human Adenovirus (HAdV) in the Post-HCT Period. Open Forum Infectious Diseases. 2025; 12(Supplement_1):ofae631.198.

Boldt, A; Bender, J; Jodele, S; Davies, SM; Benoit, SW. Differential Filtration of Macromolecules: A Novel Indicator of Mortality Risk in Pediatric HSCT Patients. Transplantation and Cellular Therapy. 2025; 31(2):s145-s146.

Bosticardo, M; Dobbs, K; Delmonte, OM; Martins, AJ; Pala, F; Kawai, T; Kenney, H; Magro, G; Rosen, LB; Yamazaki, Y; Villa, A; Rosenzweig, SD; Pittaluga, S; Notarangelo, LD. Multiomics dissection of human RAG deficiency reveals distinctive patterns of immune dysregulation but a common inflammatory signature. Science immunology. 2025; 10(103):eadq1697.

Bowers, K; Benoit, S; Rose, J; Beck, AF; Folger, AT; Calhoun, TN; Day, ME; Lovell, A; Amin, M. High Household Transmission Among Asymptomatic Contacts Across Pandemic Waves in Cincinnati, Ohio. Epidemiologia. 2025; 6(4).

Brown, M; Grassia, K; Miller, J; Hall, E; Dewan, M; Dandoy, C; Zhang, B; Wagner, AF. 1187: ECMO IN PEDIATRIC ONCOLOGIC AND HEMATOPOIETIC STEM CELL TRANSPLANT PATIENTS: A COMPARATIVE ANALYSIS. Critical Care Medicine. 2025; 53(1).

Brumm, VL; Kidd, SA; Logan, BR; Chunara, F; Heimall, J; Griffith, LM; Kohn, DB; Sanchez, L; Bednarski, JJ; Martinez, C; Pulsipher, MA; Puck, JM; Cowan, MJ; Shah, AJ. Neurodevelopmental outcomes following hematopoietic cell transplantation for patients with severe combined immunodeficiency (SCID): A PIDTC study. Journal of Human Immunity. 2026; 2(1):e20250163.

Butt, H; Dwivedi, P; Davila Saldana, B; Kochis, S. Etiologies and clinical predictors of pediatric eosinophilia: A retrospective analysis from a tertiary care center. Blood. 2025; 146(Supplement 1):6554-6554.

Chandra, S; Greis, KD; Chutipongtanate, S; Luebbering, N; Webster, A; Poisson, K; Fisher, K; Smiley, K; Marsh, RA; Jordan, MB; Davies, SM. Novel CSF Biomarkers for facilitating diagnosis of CNS-HLH from other Neuroinflammatory Disorders. Blood advances. 2025.

Chandrakasan, S; Allen, CE; Bhatla, D; Carter, J; Chien, M; Cooper, R; Draper, L; Eckstein, OS; Hanna, R; Hays, JA; Walkovich, KJ; Yee, JD; Zoref-Lorenz, A; Behrens, EM. Emapalumab Treatment in Patients With Rheumatologic Disease-Associated Hemophagocytic Lymphohistiocytosis in the United States: A Retrospective Medical Chart Review Study. Arthritis & Rheumatology. 2025; 77(2):226-238.

Chiang, S; Yang, L; Akeno, N; Owsley, E; De Jesus, A; Goldbach-Mansky, R; Marsh, R; Bleesing, J. Validation of an Interferon Type I Score Test on the Nanostring nCounter Platform. Journal of Human Immunity. 2025; 1(CIS2025).

Chiang, S; Akeno, N; Owsley, E; Verbsky, J; Ibrahimova, A; Bleesing, J; Marsh, R. Clinical and Analytical Validation of a NOD2 Functional Test for XIAP/XLP2 Diagnosis. Journal of Human Immunity. 2025; 1(CIS2025).

Chiang, SCC; Owsley, E; Husami, A; Akeno, N; Cobb, CM; Yang, L; Marsh, RA; Myers, KA; Rubin, TS. Case Report: A patient with a novel heterozygous IRF8 variant with repeated infection and immune-mediated organ disease, but without disseminated mycobacterial disease despite BCG immunization. Frontiers in Immunology. 2025; 16:1654617.

Chiang, SCC; Yang, L; Owsley, E; Husami, A; Akeno, N; Cobb, C; Hartog, NL; Elizalde, A; Seroogy, CM; Blanchard-Rohner, G; Marsh, R; Bleesing, J; Jordan, MB; Marwaha, AK. Lipopolysaccharide-responsive and beige-like anchor protein (LRBA) functional deficiency caused by biallelic LRBA missense variants characterized by Evans syndrome or colitis. Journal of Allergy and Clinical Immunology. 2025; 156(2):270-278.

Choi, J; Koo, J. Yellow Fluorescent Protein Quenching Assay for Analyzing Odorant Receptor Activity. Methods in Molecular Biology. 2025; 2915:169-177.

Choi, J; Koo, J. Protein-Protein Interactions of Odorant and G Protein-Coupled Receptors: A BRET Analysis Approach. Methods in Molecular Biology. 2025; 2915:161-168.

Chowdhury, I; Jakobsen, ER; Krupski, M. A strongly degenerate fully nonlinear mean field game with nonlocal diffusion. Journal of Differential Equations. 2025; 440:113436.

Cook, E; Haacker, L; Chandra, S; Jordan, MB; Verkamp, B; Mccarthy, L; Rotz, SJ; Hammoud, MS; Pariury, H; Mckeone, D; Kumar, A. EBV-Associated T/NK-LPD Manifesting As HLH Cured By Nivolumab and Emapalumab, Avoiding the Need for Allogeneic HCT. Transplantation and Cellular Therapy. 2025; 31(2):s43.

Cook, E; Schulert, G; Grom, A; Towe, C; Burg, G; Marsh, R; Chandra, S. Experience with T Cell–Depleted Allogeneic HSCT for Refractory sJIA Associated with Lung Disease. Journal of Human Immunity. 2025; 1(CIS2025).

Cook, E; Rotz, SJ; Auletta, JJ; Bidgoli, A; Blacken, R; Johnson, D; Badia, P; French, K; Hartley, DM; Kent, GR; Schoettler, ML; Sampson, M; Dandoy, CE; Fitch, TJ. Central Venous Catheter Removal After Hematopoietic Stem Cell Transplant: A Review and Perspective. Pediatric Blood and Cancer. 2025; e70001.

Cook, E; Langenberg, L; Luebbering, N; Ibrahimova, A; Myers, KC; Sabulski, A; Dandoy, C; Lake, K; Ziady, A; Lane, A; Webster, A; Abdullah, S; Jodele, S; Davies, SM. Oxidative Stress Early After Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31(3):135.e1-135.e10.

Dandoy, CE; Auletta, JJ; Badia, P; Bidgoli, A; Daraiseh, NM; Desalvo, AM; Diaz, J; Davies, SM; Demmel, K; Cook, E; Salem, BM; Snyder, A; Juckett, M; Hartley, D. Engraft: A Collaborative Learning Health Network for Enhanced Transplant and Cellular Therapy Outcomes. Transplantation and Cellular Therapy. 2025; 31(3):123-134.

Davies, SM; Grimley, MS; Shrestha, A; Shova, A; Asnani, M; Kent, M; Sayani, F; Quinn, CT; Niss, O; Lutzko, CM; Witting, S; Latham, T; Bushman, FD; Malik, P. Gene Therapy with Reduced-Intensity Conditioning for Sickle Cell Disease. Transplantation and Cellular Therapy. 2025; 31(2):s2-s3.

Dávila Saldaña, BJ; Schultz, KR; Ramgopal, A; Boiko, JR; Beebe, K; Carpenter, PA; Chan, SS; Paczesny, S; Aguayo-Hiraldo, P; Cuvelier, GDE; Rotz, SJ; Duncan, CN; Williams, KM. Pediatric Transplant and Cellular Therapy Consortium RESILIENT Conference on Pediatric Chronic Graft-versus-Host Disease Survivorship after Hematopoietic Cell Transplantation: Part II. Organ Dysfunction and Immune Reconstitution Considerations for Children with Chronic Graft-versus-Host Disease after Hematopoietic Cell Transplantation. Transplantation and Cellular Therapy. 2025; 31(6):347.e1-347.e17.

Dei-Adomakoh, YA; Segbefia, CI; Latham, TS; Lane, AC; Dzefi-Tettey, K; Amissah-Arthur, K; Corquaye, O; Korang, L; Mensah, E; Ekpale, P; Seedah, D; Stuber, SE; Smart, LR; Ware, RE. Hydroxyurea for Children and Adults with Hemoglobin SC Disease. NEJM Evid. 2025; 4(2):EVIDoa2400402.

Desalvo, A; Ragon, B; Bhatt, N; Hamilton, BK; Borogovac, A; Horowitz, M; Khera, N; Juckett, M; Devine, S; Dandoy, C; Wall, S; Stewart, V; Heuer, M; Molfenter, T. Upstream integration of implementation planning in clinical trials through the blood and marrow transplant clinical trials network. Blood. 2025; 146(Supplement 1):7913-7913.

Djassemi, N; Kinoshita, H; Maghzian, N; Datar, A; Joy, E; Mccann, C; Shibli, A; Saldana, BD; Hoq, F; Hanley, PJ; Pulsipher, MA; Bollard, CM; Keller, MD. Outcome Analysis Post Virus-Specific T Cell Therapy for the Treatment of Adenoviremia in Immunocompromised Pediatric Patients. Transplantation and Cellular Therapy. 2025; 31(2):s221-s222.

Drozdov, D; Luo, X; Marsh, RA; Abraham, RS; Ebens, CL. Relevance of Recent Thymic Emigrants Following Allogeneic Hematopoietic Cell Transplantation for Pediatric Patients with Inborn Errors of Immunity. Transplantation and Cellular Therapy. 2025; 31(4):265.e1-265.e12.

Durkee-Shock, J; Cohen, A; Maghzian, N; Pezzella, G; Jensen-Wachspress, M; Hostal, A; Barton, K; Gangler, K; Dávila Saldaña, BJ; Chaimongkol, N; Gonzalez, C; Notarangelo, LD; Green, KY; Keller, MD. Reconstitution of Norovirus-Specific T-Cell Responses Following Hematopoietic Stem Cell Transplantation in Patients With Inborn Errors of Immunity and Chronic Norovirus Infection. Journal of Infectious Diseases. 2025; 231(3):773-783.

Fidler, AL; O'connor, G; Beebe, DW; Wang, YM; Crosby, LE; Dandoy, CE. How to Improve the Sleep of Hospitalized Pediatric Patients: Family and Staff Focus Groups. Transplantation and Cellular Therapy. 2025; 31(8):586.e1-586.e11.

Fragneau, R; Fraitag, S; Kemps, PG; Hélias-Rodzewicz, Z; Roy, S; Bonsang, B; Bartlett, AL; Dhar, S; Jankofsky, M; Zlocha, J; Donadieu, J; Borkhardt, A; Picarsic, JL; Emile, J-F. NTRK1-rearranged histiocytosis: clinicopathologic and molecular features. Blood advances. 2025; 9(14):3617-3628.

Galletta, TJ; Benoit, SW; Markham, J; Pillay-Smiley, N; Queen, K; Graham, RT. Elevated Bromide Levels Due to Tazemetostat Therapy Treated With Salt and Water Supplementation in Two Children With Atypical Teratoid Rhabdoid Tumor. Pediatric Blood and Cancer. 2025; 72(8):e31803.

Ghalehsari, N; Pandey, M; Auletta, JJ; Beaver, E; Davies, SM; Espinoza-Gutarra, MR; Fraint, E; Holter-Chakrabarty, J; Howard, D; Knutson, J; Ramos, KN; Shah, R; Hall, AG; Gomez-Arteaga, A. Physician Advocacy for Hematopoietic Cell Transplantation and Cell Therapy: Overcoming Challenges to Reduce Disparities and Improve Outcomes for Patients. Transplantation and Cellular Therapy. 2026; 32(1):12.e1-12.e4.

Gilliam, CA; Deblasio, D; Poynter, SE; Vukovic, AA; Kinnear, B. Reprioritizing and embracing change: Implications of the ACGME revised requirements on pediatric medical education and hospital medicine. Journal of Hospital Medicine. 2025; 20(9):1009-1011.

Ginocchio, MP; Gutarra, ME; Ramos, KN; Shah, R; Pandey, M; Ghalehsari, N; Davies, SM; Auletta, JJ; Hall, AG; Arteaga, AG. Understanding Diversity: An ASTCT-NMDP Access Initiative Survey of the Hematopoietic Cell Transplant and Cellular Therapy Nonphysician Workforce. Transplantation and Cellular Therapy. 2025; 31(2):s343-s344.

Ginocchio, MP; Ramos, KN; Gutarra, ME; Ghalehsari, N; Pandey, M; Shah, R; Davies, SM; Auletta, JJ; Arteaga, AG; Hall, AG. Physician Workforce Diversity in the Hematopoietic Cell Transplant and Cellular Therapy Ecosystem: An ASTCT-NMDP Access Initiative Survey. Transplantation and Cellular Therapy. 2025; 31(2):s361.

Gower, WA; Tamae-Kakazu, M; Shanthikumar, S; Srinivasan, S; Reardon, EE; Barochia, AV; Charbek, E; Calvo, C; Cheng, PC; Das, S; Sheshadri, A; Towe, CT; Goldfarb, SB; Iyer, NP. Pulmonary function testing in pediatric allogeneic stem cell transplant recipients to monitor for Bronchiolitis obliterans syndrome: a systematic review. BMC Pediatrics. 2025; 25(1):250.

Grassia, KL; Diseroad, E; Jodele, S; Dandoy, CE; Towe, C; Davies, SM; Sabulski, A. Managing Diffuse Alveolar Hemorrhage in Pediatric HSCT with Inhaled and Intrabronchial Therapy: A Case Series of Targeted Hemostatic Intervention. Transplantation and Cellular Therapy. 2025; 31(2):s153.

Grimley, M; Davies, SM; Shrestha, A; Shova, A; Asnani, M; Kent, M; Sayani, F; Quinn, CT; Niss, O; Lutzko, C; Witting, S; Latham, T; Bushman, FD; Malik, P. Lentiviral gene therapy with reduced-intensity conditioning for sickle cell disease: a phase 1/2 trial. Nature Medicine. 2025; 31(7):2204-2212.

Grupp, S; Grimley, M; Driscoll, T; Mahadeo, K; Leonard, A; Wang, Y; Phillips, H; Justus, D; Lehmann, L; Esrick, E; Tisdale, J; Sharma, A; Crees, Z; Manis, J. Improved hematopoietic stem cell mobilization for gene therapy using single agent motixafortide in sickle cell disease. Blood. 2025; 146(Supplement 1):2542-2542.

Hahn, TE; Zhao, Q; Miller, EG; Elder, P; Langenberg, L; Davies, SM; Bejanyan, N; Vasu, S. Incidence of Transplant-Associated Thrombotic Microangiopathy (TA-TMA) Is Not Lowered By Reduction of Acute GvHD (aGvHD) in Patients Receiving Post-Transplant Cyclophosphamide (PTCy) GvHD Prophylaxis: A Report from the MIDAS (Microangiopathy, Endothelial Damage in Adults undergoing Stem cell transplantation) Consortium. Transplantation and Cellular Therapy. 2025; 31(2):s282.

Haney, M; Ashraf, A; Lake, KE; Strecker, L; Myers, KC; Towe, C; Walkup, L; Woods, J; Edwards, SL; Cooper, R; Goldfarb, SB; Davies, SM; Koo, J; Groups, T. Community respiratory viruses are generally welltolerated in hematopoietic stem cell transplant recipients: a brief report from the TRANSPIRE study. Haematologica. 2025; 110(8):1882-1886.

Huber, J; Auletta, JJ; Cook, E; Culbertson, C; Diaz, J; Fitch, T; Flesch, L; French, K; Jaglowski, S; Jodele, S; Snyder, AJ; Hartley, D; Dandoy, CE; Liang, WH. Establishing the Engraft Multi-Center Tri-Use Registry. Transplantation and Cellular Therapy. 2025; 31(2):s529-s530.

Hudda, Z; Webster, A; Anderson, E; Badia, P; Bagatell, R; Bhar, S; Bidgoli, A; Boyd, K; Chaudhury, S; Cisneros, GS; Weiss, BD; Yazdani, S; Zheng, D; Dandoy, CE. Acute Toxicities and Early Outcomes of Tandem Autologous Stem Cell Transplantation in Pediatric High-Risk Neuroblastoma: A Multicenter Study. Transplantation and Cellular Therapy. 2025.

Hudda, Z; Schoettler, ML; Rotz, SJ; Kapadia, M; Lehmann, LE; Freedman, JL; Pater, L; Weiss, B; Badia, P; Davies, SM; Mormann, M; Desai, A; Webster, A; Dandoy, CE. Acute Toxicities and Early Outcomes of Tandem Autologous Stem Cell Transplantation in Pediatric High-Risk Neuroblastoma: A Multicenter Study. Transplantation and Cellular Therapy. 2025; 31(2):s93-s94.

Hudda, Z; Davies, SM; Lane, A; Schiff, DE; Anderson, EJ; Mehta, PA; Myers, KC; Gloude, NJ. Abatacept Prevents Severe Acute Graft-Versus-Host Disease Without Increasing Graft Failure Risk in Pediatric Bone Marrow Failure Syndromes. Pediatric Blood and Cancer. 2025; 72(12):e32085.

Hudda, Z; Flannery, A; Dillhoff, P; Webster, K; Jacobs, J; Strong, S; Detzel, J; Davies, SM; Khandelwal, P. Chronic Graft-Versus-Host Disease Adversely Impacts School Performance in Children and Young Adults. Transplantation and Cellular Therapy. 2025; 31(2):99.e1-99.e11.

Hudda, Z; Lawhorn, E; Mani, B; Badia, P; Frias, O; Myers, KC; Howell, JC; Burns, K. Longitudinal Outcomes of Fertility Potential in Female Pediatric and Young Adult Allogeneic Hematopoietic Stem Cell Transplant Survivors. Transplantation and Cellular Therapy. 2025; 31(2):s98.

Hussain, M; Nagarsheth, N; Jones, J; Bleesing, J; Chandra, S; Marsh, R; Dansereau, C; O'donnell, M; Silva, O; Kerwin, B; De Ravin, SS; Prockop, S; Williams, D; Pai, S-Y. A Novel Dominant Negative Variant in IL2RG Gene that Failed to Be Corrected by Lentiviral Gene Therapy. Journal of Human Immunity. 2025; 1(CIS2025).

Hyeong, J; Koo, J; Rim, M; Wi, Y; Ko, H; Yu, D; Kim, S; Kim, N; Yoo, MJ; Jeong, K-U. Stretchable Heat Transfer Eco-Materials: Mesogen Grafted NR-Based Nanocomposites with High Thermal Conductivity and Low Dielectric Constant. Small. 2025; 21(2):e2406066.

Ibrahimova, A; Bidgoli, A; Ashraf, A; Krogman, A; Klink, G; Teusink-Cross, A; Schoettler, ML; Davies, SM; Khandelwal, P. Real world experience using belumosudil for treatment of chronic graft versus host disease in children and young adults. Bone Marrow Transplantation. 2026.

Ibrahimova, A; Khoury, R; Jodele, S; Grimley, M; Davies, SM; Khandelwal, P. Abatacept for acute graft versus host disease prophylaxis in children with sickle cell disease patients undergoing HLA identical sibling hematopoietic stem cell transplantation. Bone Marrow Transplantation. 2025; 60(8):1102-1107.

Ibrahimova, A; Luebbering, N; Langenberg, L; Abdullah, S; Strecker, L; Lake, KE; Lane, A; Webster, A; Myers, KC; Jodele, S; Davies, SM. Kinetics of DNases after hematopoietic stem cell transplant. Blood Vessels, Thrombosis & Hemostasis. 2025; 2(2):100055.

Ibrahimova, A; Ashraf, A; Klink, G; Teusink-Cross, A; Davies, SM; Khandelwal, P. Single Center Experience of Belumosudil in Children < 12 Years, Adolescents and Young Adults. Transplantation and Cellular Therapy. 2025; 31(2):s305-s306.

Jodele, S. Targeting the lectin pathway in TA-TMA. Blood advances. 2026; 10(1):181-182.

Jodele, S; Gavriilaki, E. Translating biomarker insights into practice: a path forward in TA-TMA management. Frontiers in Medicine. 2025; 12:1550365.

Josephson, M; Boas, H; Freedman, J; Young, LR; Goldfarb, SB; Robinson, PD; Towe, C; Gaffin, JM; Wong, W; Koo, J; Lane, A; Davies, SM; Mc Donough, J; Allen, JL. Intrabreath Oscillometry (IBO) vs. Spectral Oscillometry (SO) in Detecting Respiratory Disease in Patients Undergoing Hematopoietic Stem Cell Transplantation (HSCT) American Journal of Respiratory and Critical Care Medicine. 2025; 211(Supplement_1):a5118-a5118.

Khandelwal, P; Fish, JD; Gorfinkel, L; Guilcher, GMT; Howell, J; Nishitani, M; Nuechterlein, B; Obeng, E; Shah, AJ; Cuvelier, GDE; Rotz, S; Williams, KM; Duncan, CN. Pediatric Transplant and Cellular Therapy Consortium RESILIENT Conference on Pediatric Chronic Graft-versus-Host Disease Survivorship after Hematopoietic Cell Transplantation: Part III. Long-Term Impact of Chronic Graft-versus-Host Disease on Endocrinologic, Cardiovascular, and Metabolic Outcomes in Survivors of Pediatric Hematopoietic Cell Transplantation. Transplantation and Cellular Therapy. 2025; 31(5):297.e1-297.e15.

Khandelwal, P; Ibrahimova, A; Lane, A; Grimley, M; Davies, SM; Jodele, S. Abatacept improves posttransplant survival and reduces endothelial injury syndromes in β-thalassemia major. Blood advances. 2025; 9(24):6370-6379.

Khoury, R; Jordan, M; Bleesing, J; Kumar, A; Saldana, BD; Verkamp, B; Davies, S; Marsh, R; Chandra, S. Addition of Thiotepa to Alemtuzumab, Fludarabine, and Melphalan Reduced-Intensity Conditioning Reduces Secondary Graft Failure in Allogeneic HSCT for Inborn Errors of Immunity. Journal of Human Immunity. 2025; 1(CIS2025).

Konduri, M; Boe, D; Yazigi, N; Khan, K; Ward, BR; Saldana, BD; Cavener, D; Kallakury, B; Kroemer, A; Matsumoto, C; Fishbein, T; Ekong, UD. Wolcott-Rallison syndrome - crosstalk between PERK- EIF2A and type II interferon signaling. European Journal of Medical Genetics. 2025; 76:105022.

Koo, J; Webster, A; Lake, KE; Luebbering, N; Dandoy, C; Jodele, S; Ryan, TD; Davies, SM; Sabulski, A. Proteomic analysis of pericardial effusions in hematopoietic stem cell transplant recipients. Haematologica. 2025.

Koo, J; Webster, A; Dandoy, CE; Jodele, S; Davies, SM; Sabulski, A. The Tell-Tale Heart: A Cytokine Storm Story of Pericardial Effusions after HSCT. Transplantation and Cellular Therapy. 2025; 31(2):s137.

Koo, J; Cooper, R; Edwards, SL; Lane, A; Loveless, SK; Strecker, L; Lake, KE; Myers, KC; Towe, C; Patti, J; Li, M; Goldfarb, SB; Woods, JC; Davies, SM. High Prevalence of Abnormal Baseline Lung Function in Pediatric and Young Adult Hematopoietic Stem Cell Transplant Recipients: A Report from the TRANSPIRE Study. Pediatric Blood and Cancer. 2025; 72(10):e31916.

Koo, J; Snyder, AJ; Campbell, K; Miller, E; O'conner, A; Grompe, M; Mehta, PA; Myers, KC; Davies, SM. Hepatocyte senescence and persistent liver injury in Fanconi anemia. Haematologica. 2025; 110(8):1870-1874.

Koo, J; Webster, A; Myers, KC; Davies, SM; Davies, SM; Sabulski, A. Transcriptomic Alterations and Clonal Evolution Identifies a Pre-Emptive Indication for Hematopoietic Stem Cell Transplant in Fanconi Anemia. Transplantation and Cellular Therapy. 2025; 31(2):s308-s309.

Koo, J; Lake, KE; Langenberg, L; Anderson, J; Edwards, SL; Teusink-Cross, A; Romick-Rosendale, L; Sabulski, A; Jodele, S; Davies, SM. Pravastatin Prophylaxis Is Safe and Feasible in Children and Young Adults Undergoing Allogeneic HSCT: A Prospective, Single Arm Cohort Study. Transplantation and Cellular Therapy. 2025; 31(2):s153-s154.

Koo, J; Miller, E; O'conner, A; Campbell, KM; Grompe, M; Myers, KC; Mehta, PA; Davies, SM. Beyond Graft-Vs-Host Disease: The Role of Cellular Senescence in Persistent Liver Injury in Fanconi Anemia after HSCT. Transplantation and Cellular Therapy. 2025; 31(2):s311-s312.

Koo, J; Langenberg, L; Zhao, X; Setchell, KR; Lake, KE; Luebbering, N; Walter, E; Lane, A; Myers, KC; Reynaud, D; Sabulski, A; Teusink-Cross, A; Jodele, S; Davies, SM. Lipid dysregulation after hematopoietic stem cell transplant. Haematologica. 2025.

Koo, J; Haney, M; Schwarz, D; Kim, J; Schwarz, L; Steltz, S; Korn, E; Cheng, L; Loveless, S; Cooper, R; Shimamura, A; Myers, K; Grover, A; Wehrman, A. Liver disease in shwachman-diamond syndrome: A report from the shwachman-diamond syndrome registry. Blood. 2025; 146(Supplement 1):1436.

Koo, J; Hornung, LN; Howell, J; Lawhorn, E; Comstock, D; Reilly, C; Ferrer, A; Mangaonkar, A; Barredo, B; Churpek, J; Patel, B; Savage, S; Giri, N; Myers, K. Bone matters: Defining the burden of skeletal disease in telomere biology disorders. Blood. 2025; 146(Supplement 1):6747.

Koo, J; Myers, KC. Immunodeficiency in TBDs: making the lymphocyte count. Blood. 2025; 146(10):1148-1150.

Kusoski, C; Mehta, PA; Markham, J; Zhao, J; Setchell, KDR; Murphy, M; Teusink-Cross, A. Utilization of Intravenous Posaconazole in Pediatric Patients Undergoing Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31(12):1033.e1-1033.e11.

Kusoski, CL; Mehta, PA; Markham, J; Murphy, M; Teusink-Cross, A. Higher Dose Intravenous Posaconazole Is Safe and Necessary for Achievement of Therapeutic Targets and Prevention of Infections in Pediatric Hematopoietic Stem Cell Transplant Patients. Transplantation and Cellular Therapy. 2025; 31(2):s546.

Lane, A. Optimal relevant subset designs in nonlinear models. Canadian Journal of Statistics, The. 2025; 53(3).

Langenberg, L; Abdullah, S; Lies, E; Benoit, SW; Ramos, KN; Jodele, S; Davies, SM; Sabulski, A. Urine Kidney Injury Biomarkers Predict TMA Risk in Pediatric HSCT Recipients. Transplantation and Cellular Therapy. 2025; 31(2):s314.

Langenberg, L; Jodele, S; Davies, SM; Sabulski, A. Supar Is a Novel and Powerful Biomarker of TMA and Kidney Injury after HSCT. Transplantation and Cellular Therapy. 2025; 31(2):s313-s314.

Lichtenstein, DA; Sridharan, A; Khoury, R; Grimley, MS; Rubinstein, JD; Lutzko, CM; Wang, YM. Effect of Clinically Relevant Immunosuppressants on Viral Specific T-Cell (VST) in Vitro Function. Transplantation and Cellular Therapy. 2025; 31(2):s509-s510.

Liu, B; Sajiki, Y; Littlefield, N; Hu, Y; Stuart, WD; Sridharan, A; Cui, X; Siefert, ME; Araki, K; Ziady, AG; Shi, D; Whitsett, JA; Maeda, Y. PBAE-PEG-based lipid nanoparticles for lung cell-specific gene delivery. Molecular Therapy. 2025; 33(3):1154-1165.

Macaraeg, M; Baker, E; Handorf, E; Matt, M; Baker, EK; Brunner, H; Grom, AA; Henrickson, M; Huggins, J; Zhang, W; Lee, P; Marsh, R; Schulert, GS. Clinical, Immunologic, and Genetic Characteristics in Patients With Syndrome of Undifferentiated Recurrent Fevers. Arthritis & Rheumatology. 2025; 77(5):596-605.

Maier, S; Auletta, JJ; Badia, P; Cook, E; Craddock, JA; Culbertson, C; Daraiseh, N; Davies, SM; Desalvo, AM; Diaz, J; Nishitani, M; Snyder, AJ; Dandoy, CE; Parker, L. Establishing a Quality Improvement Education Platform in the Engraft Learning Network. Transplantation and Cellular Therapy. 2025; 31(2):s501.

Mani, B; Hudda, Z; Lawhorn, E; Frias, O; Myers, K; Burns, K; Howell, JC. SAT-218 Longitudinal outcomes of fertility potential in female pediatric hematopoietic stem cell transplant survivors. Journal of the Endocrine Society. 2025; 9(Supplement_1):bvaf149.1785.

Manjrekar, P; Sabulski, A; Lies, E; Dandoy, CE; Davies, SM; Laskin, B; Jodele, S. The HCT Protein Shake: Moderate and Severe Proteinuria Are Specific to TA-TMA. Transplantation and Cellular Therapy. 2025; 31(2):s145.

Maron, G; Boeckh, MJ; Papanicolaou, G; Gomez, C; Prasad, V; Dara, J; Elgarten, C; Kumar, M; Wynn, R; Lion, T; Fukushima, K; Maher, R; Azie, N; Grimley, M. P-103. Adenoviremia Clearance Following Treatment with Intravenous (IV) Brincidofovir (BCV) in Immunocompromised Patients is Associated with Positive Clinical Disease Response: Preliminary Outcomes from the ATHENA Phase IIa Study. Open Forum Infectious Diseases. 2025; 12(Supplement_1):ofae631.310.

Marsh, R; Khoury, R; Mizuno, K; Hosawi, A; Cottrell, C; Nguyen, E; Landon, B; Chandra, S; Jordan, M; Kumar, A; Bleesing, J; Davies, S; Moore, C; Mehta, P. Precision Alemtuzumab Dosing Results in Day 0 Target Range Achievement in 80% of IEI Patients and Minimizes Risks of GVHD, Clinically Significant Mixed Chimerism, and Secondary Graft Failure. Journal of Human Immunity. 2025; 1(CIS2025).

Marsh, RA; Bleesing, JJ; Chiang, SCC. Diagnostic testing for hemophagocytic lymphohistiocytosis. Journal of Immunological Methods. 2025; 537:113816.

Matt, MG; Drozdov, D; Bendstrup, E; Glerup, M; Hauge, E-M; Masmas, T; Schneider, EC; Zeilhofer, UB; Abu-Arja, RF; Driest, KD; Chandra, S; Grom, A; Schulert, GS; Marsh, RA. Allogeneic haematopoietic stem-cell transplantation for children with refractory systemic juvenile idiopathic arthritis and associated lung disease: outcomes from an international, retrospective cohort study. The Lancet Rheumatology. 2025; 7(4):e243-e251.

Maurer, A; Wang, T; Defilipp, Z; Devos, J; Farhadfar, N; Khandelwal, P; Spellman, S; El Jurdi, N; Lee, S; Soiffer, R. Reduced chronic graft versus host disease after allogeneic HSCT with cryopreserved peripheral blood stem cell grafts: A CIBMTR analysis. Blood. 2025; 146(Supplement 1):933-933.

Mccormack-Spivey, S; Sabulski, A; Davies, SM; Chandra, S. Defining and Assessing Poor Graft Function after Allogeneic HSCT in Children and Young Adults. Transplantation and Cellular Therapy. 2025; 31(2):s317-s318.

Mccormack-Spivey, S; Laskin, B; Seif, AE; Blackard, JT; Odegard, E; Kleiboeker, S; Jodele, S; Bourgeois, T; Zee, J; Davies, SM; Sabulski, A. The First Prospective Screening Study of BK Polyomavirus (BKPyV) Hemorrhagic Cystitis after HSCT. Transplantation and Cellular Therapy. 2025; 31(2):s513-s514.

Mccormack-Spivey, S; Strecker, L; Webster, A; Davies, SM; Sabulski, A. Plasma LILRA6 Levels Influence BK Polyomavirus Cystitis after HSCT. Transplantation and Cellular Therapy. 2025; 31(2):s514-s515.

Mehta, PA; Nelson, A; Loveless, S; Lane, A; Fukuda, T; Teusink-Cross, A; Elder, D; Lagory, D; Miller, E; Cancelas, JA; Edwards, S; Chihanga, T; Wells, SI; Davies, SM. Phase 1 study of quercetin, a natural antioxidant for children and young adults with Fanconi anemia. Blood advances. 2025; 9(8):1927-1939.

Merli, P; Jodele, S; Cook, E; Myers, KC; Lane, A; Ryhänen, S; Cefalo, MP; Quagliarella, F; Davies, SM; Teusink-Cross, A; Kohorst, M; Corsetti, T; Locatelli, F; Sabulski, A. Emapalumab for the Treatment of Immune-Mediated Graft Failure after HSCT. Bone Marrow Transplantation. 2025; 60(3):406-411.

Meyer, R; Orndorff, L; Engel, H; Hoback, P; Spivey, S; Mikut, K; Spears, K; Clark, A; Sarver, S; Dandoy, CE. Nurse Driven Central Line Rounding Utilized to Improve Bone Marrow Transplant Patient Outcomes: An Update. Transplantation and Cellular Therapy. 2025; 31(2):s451.

Mizuno, K; Teusink-Cross, A; Sabulski, A; Davies, SM; Jodele, S. Unraveling the Challenges of Non-Responders to the Eculizumab Treatment with High-Risk Hematopoietic Stem Cell Transplant-Associated Thrombotic Microangiopathy (TA-TMA) Transplantation and Cellular Therapy. 2025; 31(2):s542-s543.

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Murphy, CR; Liu, C; Courter, J; Griffin, C; Scaggs Huang, F; Miller-Handley, H; Grimley, MS; Danziger-Isakov, L; Otto, WR. Receipt of Fluoroquinolone Prophylaxis is not Associated With Development of Vancomycin-Resistant Enterococcus Colonization During Pediatric Hematopoietic Cell Transplantation. Journal of the Pediatric Infectious Diseases Society. 2025; 14(3).

Myers, KC; Andresen, F; Goldberg, B; Weller, E; Reilly, C; Nakano, TA; Bertuch, AA; Geddis, A; Joos, M; Coyne, K; Brundige, K; Loveless, S; Cheng, L; Shimamura, A. SUPERIOR SURVIVAL FOLLOWING HEMATOPOIETIC STEM CELL TRANSPLANTATION FOR HIGH-RISK MARROW FEATURES IN PATIENTS WITH SHWACHMAN-DIAMOND SYNDROME. EJC Paediatric Oncology. 2025; 6:100336.

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Naymagon, L; Roehrs, P; Hermiston, M; Connelly, J; Bednarski, J; Boelens, J-J; Chandrakasan, S; Dávila Saldaña, B; Henry, MM; Satwani, P; Teachey, D; Behrens, EM; Canna, SW; Kumar, A. Perspectives on the current diagnostic and treatment paradigms in secondary hemophagocytic lymphohistiocytosis (HLH). Orphanet Journal of Rare Diseases. 2025; 20(1):200.

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Nguyen, TH; Satwani, P; Kumar, D; Kapoor, U; Malik, S; Prince, C; Montminy, T; Smiley, K; Martinez, M; Goldner, D; Fazlollahi, L; Rytting, HB; Romero, R; Chandrakasan, S. Systemic T-cell activation and IFN-γ activity in indeterminate severe hepatitis are reminiscent of hemophagocytic lymphohistiocytosis: Implications for T-cell- and IFN-γ-directed therapies. Journal of Allergy and Clinical Immunology. 2025; 155(1):199-212.

Nieves, RM; Latham, T; Marte, N; Berges, M; Sánchez, LM; Urcuyo, G; Florencio, C; Gonzalez, C; Del Villar, P; Chen, S; Schultz, WH; Lane, AC; Mena, R; Ware, RE. Stroke prevention in Hispanic children with sickle cell anemia: the SACRED trial. Blood advances. 2025; 9(8):1791-1800.

Oved, JH; Marsh, RA; Petrovic, A. Haematopoietic stem cell transplant for inborn errors of immunity-Who and when? British Journal of Haematology. 2025; 207(3):750-753.

Perales, M-A; Riches, M; He, N; Martens, MJ; Chemaly, RF; Dandoy, CE; Hill, JA; Diaz, MA; Hashmi, S; Prockop, S; Lazarus, HM; Beitinjaneh, AM; Hildebrandt, GC; Auletta, JJ; Szabolcs, P. Delayed T-cell recovery after hematopoietic cell transplantation is associated with decreased overall survival in adults. Blood advances. 2025; 9(14):3502-3517.

Pereda Ginocchio, MA; Ramos, KN; Espinoza-Gutarra, MR; Ghalehsari, N; Pandey, M; Shah, R; Davies, SM; Gomez-Arteaga, A; Hall, AG. Understanding Diversity: An ASTCT-NMDP ACCESS Initiative Survey of the Hematopoietic Cell Transplant and Cellular Therapy Workforce in the United States. Transplantation and Cellular Therapy. 2025.

Perry, C; Eldem, I; Zarnegar-Lumley, S; Shliakhtsitsava, K; Cancio, M; Myers, K; Bhatla, D; Thota, S. Transition of care of youth with bone marrow failure conditions: Current practices, barriers, and burden- a survey of hematology-oncology providers in the US. Blood. 2025; 146(Supplement 1):4394.

Phelan, R; Rotz, S; Dandoy, CE; Auletta, JJ; Badia, P; Bhatt, NS; Ballard, SA; Blacken, R; Daraiseh, NM; Desmond, C; Pai, A; Tarquini, S; Fitch, TJ; Hartley, D. Multicenter Study on Caregiver Experiences in Pediatric Hematopoietic Stem Cell Transplantation: Part II. Treatment Challenges, Communication Barriers, and Caregiver-Driven Approaches to Mitigation. Transplantation and Cellular Therapy. 2025; 31(8):590.e1-590.e16.

Potter, A; Sharma, N; Patel, K; Qureshi, MR; Khan, M; Wallace, C; Ziady, A; Ashfaq, A; Moore, C; Hayes, D. Persisting Inflammatory and Fibrotic Gene Signatures Linking Acute Cellular Rejection to Chronic Lung Allograft Dysfunction. American Journal of Transplantation. 2025; 25(8):s823-s824.

Potter, A; Sharma, N; Wallace, C; Ziady, A; Moore, C; Morales, D; Hayes, D. (750) Single Cell Technology Shines LIGHT on Acute Lung Allograft Dysfunction. The Journal of Heart and Lung Transplantation. 2025; 44(4):s355.

Potter, A; Sharma, N; Patel, K; Qureshi, M; Khan, M; Wallace, C; Ziady, A; Morales, D; Hayes, D. (276) Gene Expression Alterations in Lung Allografts with ACR and After Treatment Compared to Never ACR. The Journal of Heart and Lung Transplantation. 2025; 44(4):s140.

Power-Hays, A; Namazzi, R; Dong, M; Kazinga, C; Kato, C; Aliwuya, S; Mcelhinney, K; Conroy, AL; Lane, A; John, C; Vinks, AA; Latham, T; Opoka, RO; Ware, RE. The feasibility of pharmacokinetic-based dosing of hydroxyurea for children with sickle cell anaemia in Uganda: Baseline results of the alternative dosing and prevention of transfusions trial. British Journal of Clinical Pharmacology. 2025; 91(6):1865-1872.

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Power-Hays, A; Namazzi, R; Kato, C; Mcelhinney, KE; Conroy, AL; Hume, H; John, C; O'hara, SM; Stuber, SE; Lane, A; Latham, TS; Opoka, RO; Ware, RE. Pharmacokinetic-Guided Hydroxyurea to Reduce Transfusions in Ugandan Children with Sickle Cell Anemia: Study Design of the Alternative Dosing And Prevention of Transfusions Trial. Acta Haematologica. 2025; 148(2):208-219.

Ramos, KN; Ginocchio, MP; Gutarra, ME; Ghalehsari, N; Pandey, M; Shah, R; Davies, SM; Auletta, JJ; Arteaga, AG; Hall, AG. Perception and Reality of Racial and Ethnic Workforce Diversity in the U.S HCT/CT Workforce: Results from the ASTCT-NMDP Access Initiative Survey. Transplantation and Cellular Therapy. 2025; 31(2):s342.

Ramos, KN; Zee, J; Sabulski, A; Laskin, B; Blackard, JT; Langenberg, L; Dandoy, CE; Davies, SM; Jodele, S. Pre-Transplant Complement Activation and Transplant-Associated Thrombotic Microangiopathy (TA-TMA) across Diagnostic Groups. Transplantation and Cellular Therapy. 2025; 31(2):s25-s26.

Rangarajan, HG; Satwani, P; Herr, MM; Chen, M; Martens, MJ; Wudhikarn, K; John, S; Fabrizio, VA; Hsieh, EM; Kelkar, AH; Hill, JA; Huppler, A; Riches, M; Auletta, JJ. Real-world outcomes of infections following tisagenlecleucel in patients with B-cell ALL: a CIBMTR analysis. Blood advances. 2025; 9(21):5489-5500.

Rayes, A; Logan, BR; Liu, X; Dara, J; Buckley, RH; Oved, JH; Kapoor, N; Kapadia, M; Chandra, S; Martinez, CA; Heimall, J; Haddad, E; Pai, S-Y; Dvorak, CC. Outcomes Following Matched Sibling Donor Transplantation for Severe Combined Immunodeficiency: A Report from the PIDTC. Blood advances. 2025.

Reed, HD; Brnich, S; Gudera, J; Ditroia, S; O’Donnell-Luria, A; Li, M-J; Yang, H; Brundige, K; Loveless, S; Cheng, L; Andresen, F; Fleming, M; Myers, K; Shimamura, A. GENETIC RE-EVALUATION OF SDS-LIKE AND NEUTROPENIA CONDITIONS. EJC Paediatric Oncology. 2025; 6:100400.

Reed, HD; Do, H; Weller, E; Harris, MH; Reilly, CR; Tsai, HK; Farrar, JE; Lau, BW; Pommert, L; Gamper, C; Cheng, L; Malsch, M; Myers, K; Shimamura, A. Lymphoid malignancies in patients with Shwachman-Diamond syndrome. Blood. 2025; 145(21):2528-2532.

Reinert, S; Benoit, SW; Nagarajan, R. Long-term kidney outcomes in survivors of Wilms tumor: a single-center retrospective cohort study. Pediatric Nephrology. 2025; 40(5):1603-1611.

Riedl Khursigara, M; Benoit, S; Patriquin, CJ; Lemaire, M; Licht, C. Thrombotic Thrombocytopenic Purpura, Atypical Hemolytic Uremic Syndrome, and Spectrum of Thrombotic Microangiopathy. In: Pediatric Nephrology. Springer Nature; 2025:1-41.

Rubinstein, JD; Pham, G; Sridharan, A; Khoury, R; Wang, YM; Hudda, Z; Wilhelm, J; Lichtenstein, DA; Heyenbruch, D; Cancelas, JA; Davies, SM; Lutzko, C; Grimley, MS. Outcomes with third-party virus-specific T cells after the use of single-antigen cell lines to predict HLA restriction. Blood advances. 2025; 9(24):6305-6313.

Sabulski, A; Webster, A; Langenberg, L; Luebbering, N; Dandoy, CE; Koo, J; Jodele, S; Davies, SM. TA-TMA Evolution and Individual Susceptibility at the Proteome Level. Transplantation and Cellular Therapy. 2025; 31(2):s133.

Sampson, M; Parker, L; Dandoy, CE; Auletta, JJ; Chapman, LR; Cook, E; Craddock, J; Culbertson, C; Daraiseh, N; Diaz, J; Snyder, AJ; Staton, S; Wall, SA; Badia, P. Variation in Central Venous Catheter Practices and Complications after Stem Cell Transplant: A Multi-Center Survey of the Engraft Learning Network. Transplantation and Cellular Therapy. 2025; 31(2):s535-s536.

Samra, S; Cook, E; Wilson, J; Sharma, M; Golding, L; Yao, DT; Marsh, RA; Turvey, SE. STAT6 gain-of-function disease: p.D519N is a new disease-causing variant that responds well to dupilumab treatment. Journal of Allergy and Clinical Immunology: Global. 2025; 4(3):100494.

Sawada, K; Khandelwal, P; Davies, SM; Crooker, A; Mizuno, T; Asai, A. Pharmacokinetic Monitoring of JAK Inhibitor and Tacrolimus for Safe and Effective Management of Graft-Versus-Host Disease After Pediatric Liver Transplantation. Pediatric Transplantation. 2025; 29(7):e70187.

Schoettler, ML; Gavriilaki, E; Carreras, E; Bo-Kyoung, C; Dandoy, CE; Ho, VT; Jodele, S; Moiseev, I; Sánchez-Ortega, I; Srivastava, A; Shaw, BE; Sureda, AM; Soiffer, R; Vasu, S. An ASTCT, CIBMTR, EBMT, and APBMT Consensus Statement Defining Response Criteria for Hematopoietic Cell Transplantation Associated Thrombotic Microangiopathy (TA-TMA) Directed Therapy. Transplantation and Cellular Therapy. 2025; 31(9):610-623.

Schumacher, DJ; Michelson, C; Winn, A; Henry, D; O'connor, M; Li, S-TT; Blair, RJ; Velazquez-Campbell, M; Kihlstrom, MJ; Borman-Shoap, E; Kravtchenko, S; Jain, S; Vu, T; Schwartz, A. Graduating Residents' Readiness for Unsupervised Practice. Pediatrics. 2025; 155(5).

Schwarz, L; Cheng, L; Steltz, S; Schwarz, D; Korn, E; Loveless, S; Cooper, R; Dusa, C; Hornung, L; Howell, JC; Shimamura, A; Myers, KC; Koo, J. Growth Patterns in Shwachman-Diamond Syndrome: Findings from the North American Shwachman-Diamond Syndrome Registry. Journal of Pediatrics. 2025; 287:114780.

Shah, NC; Ngwube, A; Suresh, T; Sowa, A; Abraham, A; Anderson, E; Andreansky, M; Bhatia, M; Chaudhury, S; Cuvelier, GDE; Krishnamurti, L; Saini, S; Skiles, J; Shenoy, S. Impact of Abatacept Inclusive Graft-Versus-Host Disease Prophylaxis in Pediatric Stem Cell Transplantation for Hemoglobinopathy. Transplantation and Cellular Therapy. 2025; 31(10):826.e1-826.e10.

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