Dai, M; Lin, Y; El-Amouri, SS; Kohls, M; Pan, D.
Comprehensive evaluation of blood-brain barrier-forming micro-vasculatures: Reference and marker genes with cellular composition.
PLoS ONE.
2018;
13:e0197379-e0197379.
El-Amouri, SS; Dai, M; Han, J; Brady, RO; Pan, D.
Normalization and Improvement of CNS Deficits in Mice With Hurler Syndrome After Long-term Peripheral Delivery of BBB-targeted Iduronidase.
Molecular Therapy.
2014;
22:2028-2037.
Dai, M; Han, J; El-Amouri, SS; Brady, RO; Pan, D.
Platelets are efficient and protective depots for storage, distribution, and delivery of lysosomal enzyme in mice with Hurler Syndrome.
Proceedings of the National Academy of Sciences of USA.
2014;
111:2680-2685.
Wang, D; El-Amouri, SS; Dai, M; Kuan, C; Hui, DY; Brady, RO; Pan, D.
Engineering a lysosomal enzyme with a derivative of receptor-binding domain of apoE enables delivery across the blood-brain barrier.
Proceedings of the National Academy of Sciences of USA.
2013;
110:2999-3004.
Pan, D; Kalfa, TA; Wang, D; Risinger, M; Crable, S; Ottlinger, A; Chandra, S; Mount, DB; Huebner, CA; Franco, RS; et al.
K-Cl Cotransporter Gene Expression during Human and Murine Erythroid Differentiation.
The Journal of biological chemistry.
2011;
286:30492-30503.
Wang, D; Zhang, W; Kalfa, TA; Grabowski, G; Davies, S; Malik, P; Pan, D.
Reprogramming erythroid cells for lysosomal enzyme production leads to visceral and CNS cross-correction in mice with Hurler syndrome.
Proceedings of the National Academy of Sciences of USA.
2009;
106:19958-19963.
Worsham, DN; Schuesler, T; von Kalle, C; Pan, D.
In vivo gene transfer into adult stem cells in unconditioned mice by lentiviral in situ delivery of a vector.
Molecular Therapy.
2006;
14:514-524.
Pan, D; Gunther, R; Duan, WM; Wendell, S; Kaemmerer, W; Kafri, T; Verma, IM; Whitley, CB.
Biodistribution and toxicity studies of VSVG-pseudotyped lentiviral vector after intravenous administration in mice with the observation of in vivo transduction of bone marrow.
Molecular Therapy.
2002;
6:19-29.
Pan, D; Shankar, R; Stroncek, DF; Whitley, CB.
Combined ultrafiltration-transduction in a hollow-fiber bioreactor facilitates retrovirus-mediated gene transfer into peripheral blood lymphocytes from patients with mucopolysaccharidosis type II.
Human Gene Therapy.
1999;
10:2799-2810.