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Anderson, AR; Strouse, JJ; Manwani, D; Brandow, AM; Vichinsky, E; Campbell, A; Leavey, PJ; Nero, A; Ibrahim, IF; Field, JJ; Rivlin, K; Thompson, AA; Tubman, VN; Walters, M. COVID-19 mRNA vaccination responses in individuals with sickle cell disease: an ASH RC Sickle Cell Research Network Study. Blood Advances. 2024; 8:4549-4553.

Aygun, B; Lane, A; Smart, LR; Santos, B; Tshilolo, L; Williams, TN; Olupot-Olupot, P; Stuber, SE; Tomlinson, G; Latham, T; Ware, RE. Hydroxyurea dose optimisation for children with sickle cell anaemia in sub-Saharan Africa (REACH): extended follow-up of a multicentre, open-label, phase 1/2 trial. The Lancet Haematology. 2024; 11:e425-e435.

Beslow, LA; Krings, T; Kim, H; Hetts, SW; Lawton, MT; Ratjen, F; Whitehead, KJ; Gossage, JR; McCulloch, CE; Clancy, M; Vethanayagam, D; Weinsheimer, S; White, AJ; Wilcox, P. De Novo Brain Vascular Malformations in Hereditary Hemorrhagic Telangiectasia. Pediatric Neurology. 2024; 155:120-125.

Beslow, LA; Vossough, A; Kim, H; Nelson, J; Lawton, MT; Pollak, J; Lin, DD M; Ratjen, F; Hammill, AM; Hetts, SW; Weinsheimer, S; White, AJ; Wilcox, P; Wilcox, P. Brain AVM compactness score in children with hereditary hemorrhagic telangiectasia. Child's Nervous System. 2024; 40:2101-2108.

Beslow, LA; White, AJ; Krings, T; Hammill, AM; Lang, SS; Baba, A; Clancy, MS; Olitsky, SE; Hetts, SW. Current Practice: Rationale for Screening Children with Hereditary Hemorrhagic Telangiectasia for Brain Vascular Malformations. American Journal of Neuroradiology. 2024; 45:1177-1184.

Betensky, M; Mosha, M; Tarango, C; Verma, A; Bhat, R; Kucine, NE; Nakano, T; Nakar, C; Woods, G; Amankwah, E; Brandão, LR; Schulman, S; Goldenberg, NA. Outcomes in children with provoked venous thrombosis and antiphospholipid antibodies: findings from the Kids-DOTT trial. Blood Advances. 2024; 8:5790-5795.

Borst, AJ; Eng, W; Griffin, M; Ricci, KW; Engel, E; Adams, DM; Dayneka, J; Cohen-Cutler, SJ; Andreoli, SM; Wu, MD; Teitelbaum, M; Zong, Z; Li, Y; Jeng, MR. Treatment practices and response in kaposiform hemangioendothelioma: A multicenter cohort study. Pediatric Blood and Cancer. 2024; 71:e30779.

Carter-Febres, M; Fenchel, M; Pomales, J; Tarango, C; Mullins, ES. Hemoglobin concentration and body mass index are determinants of plasma von Willebrand factor and factor VIII levels. Thrombosis Research. 2024; 240:109061.

Cline, H; Wei, Z; Groeneveld, DJ; Hix, JM L; Xu, X; Flick, MJ; Palumbo, JS; Poole, LG; Dockendorff, C; Griffin, JH; Luyendyk, JP. Hepatocyte-independent PAR1-biased signaling controls liver pathology in experimental obesity. Journal of Thrombosis and Haemostasis. 2024; 22:3191-3198.

Cohen, CT; Tarango, C; Powers, JM. Emicizumab use in infancy: A survey of United States Pediatric Hemophilia Treatment Center Medical Directors. Haemophilia. 2024; 30:848-851.

Coppola, T; Hughes, H; Finch, PT; Hess, JA; Wu, S; Prada, CE; Miethke, AG; Zhang, W; Kalfa, TA. Case report: Childhood erythrocytosis due to hypermanganesemia caused by homozygous SLC30A10 mutation. 2024; 3:1331485.

Costa, E; Isgrò, A; de Montalembert, M; Leufkens, HG M; Ware, RE; De Franceschi, L. Successes and pitfalls in orphan drug development for sickle cell disease. Blood Advances. 2024; 8:2455-2465.

Engel, ER; Le Cras, TD; Ricci, KW. How we use angiopoietin-2 in the diagnosis and management of vascular anomalies. Pediatric Blood and Cancer. 2024; 71:e30921.

Engel, ER; Perry, T; Block, M; Palumbo, JS; Lorts, A; Luchtman-Jones, L. Bivalirudin Monitoring in Pediatric Ventricular Assist Device and Extracorporeal Membrane Oxygenation: Analysis of Single-Center Retrospective Cohort Data 2018-2022. Pediatric Critical Care Medicine. 2024; 25:e328-e337.

Engel, ER; Wusik, K; Bright, P; Vadivelu, S; Taylor, JM; Hammill, A. Prevalence and Predictors of Hereditary Hemorrhagic Telangiectasia and Capillary-Malformation Arteriovenous Malformation Syndrome Among Children with Neurovascular Malformations. The Journal of Pediatrics. 2024; 264:113761.

Filuta, AL; Amezcua, P; Ruff, BP; Biagini, JM; Kroner, J; He, H; Brandt, EB; Martin, LJ; Palumbo, JS; Khurana Hershey, GK; Sherenian, MG. The key roles of thrombin and fibrinogen in human infant and mice atopic dermatitis models. Allergy: European Journal of Allergy and Clinical Immunology. 2024; 79:239-242.

Gatts, J; Chandra, S; Krishnan, D; Ricci, K. Medical Management of Nonmalignant Vascular Tumors of the Head and Neck: Part 1. Oral and Maxillofacial Surgery Clinics of North America. 2024; 36:103-113.

Gatts, J; Chandra, SR; Ricci, K. Medical Management and Therapeutic Updates on Vascular Anomalies of the Head and Neck: Part 2. Oral and Maxillofacial Surgery Clinics of North America. 2024; 36:115-123.

Hammill, AM; Boscolo, E. Capillary malformations. The Journal of Clinical Investigation. 2024; 134:e172842.

Harms, FL; Rexach, JE; Efthymiou, S; Aynekin, B; Per, H; Güleç, A; Nampoothiri, S; Sampaio, H; Sachdev, R; Stoeva, R; Chard, M; Klassen, M; Pries, M; Kutsche, K. Loss of TBC1D2B causes a progressive neurological disorder with gingival overgrowth. European Journal of Human Genetics. 2024; 32:558-566.

Iacobas, I; Hammill, AM. Hereditary hemorrhagic telangiectasia - pediatric review. Current Opinion in Pediatrics. 2024; 36:592-598.

Kharnaf, M; Abplanalp, WA; Young, C; Sprague, C; Rosenfeldt, L; Smith, R; Wang, D; Palumbo, JS; Morales, DL S. Unmasking the Impact of Oxygenator-Induced Hypocapnia on Blood Lactate in Veno-Arterial Extracorporeal Membrane Oxygenation. ASAIO Journal. 2024; 70:795-802.

Kharnaf, M; Zafar, F; Hogue, S; Rosenfeldt, L; Cantrell, RL; Sharma, BK; Pearson, A; Sprague, C; Leino, D; Abplanalp, WA; Morales, D; Tweddell, J; Qualls, JE; Palumbo, JS. Factor XII promotes the thromboinflammatory response in a rat model of venoarterial extracorporeal membrane oxygenation. Journal of Thoracic and Cardiovascular Surgery. 2024; 168:e37-e53.

Kim, TO; Geris, JM; Flanagan, JM; Grace, RF; Lambert, MP; O’Farrell, C; Rose, MJ; Shimano, KA; Niss, O; Neunert, C; Neufeld, EJ; Despotovic, JM; Scheurer, ME; Grimes, AB. Genetic variants in canonical Wnt signaling pathway associated with pediatric immune thrombocytopenia. Blood Advances. 2024; 8:5529-5538.

Kimbrell, B; McKenney, KD; Yeom, S; Iannotti, I; Day, A; Harmon, K; Sebold, A; Smegal, L; Kaplan, K; Daisy, C; Pinto, A; Hammill, A; Moses, MA; Comi, A. Longitudinal prospective study of Sturge–Weber syndrome urine angiogenic factors and neurological outcome. 2024; 2:120-134.

Kocoshis, TS; Kalfa, TA; Miethke, AG; Balistreri, WF; Seu, KG; Slaughter, CG; Singh, R; Mullen, M; Kocoshis, SA. Red cell abnormalities characterized by ektacytometry in children with cholestasis. Pediatric Research. 2024; 95:1035-1040.

Lendrum, EC; Smart, LR; Vukovic, AA. Pancytopenia in the Emergency Department. The Journal of Pediatrics. 2024; 272:114111.

Manning, ER; Duan, Q; Taylor, S; Ray, S; Corley, AM S; Michael, J; Gillette, R; Unaka, N; Hartley, D; Beck, AF; Riley, C; Sandoval, L; Shook, L; Steller, J. Development of a multimodal geomarker pipeline to assess the impact of social, economic, and environmental factors on pediatric health outcomes. Journal of the American Medical Informatics Association : JAMIA. 2024; 31:1471-1478.

McGrady, ME; Ignjatovic, V; Jones, S; Bruce, A; Goldenberg, NA; Rizzi, M; Thornburg, CD; Todd, KE; Luchtman-Jones, L. Evaluation, analysis, and reporting of medication adherence for clinical trials of anticoagulants in children: guidance from the ISTH SSC Subcommittee on Pediatric and Neonatal Thrombosis and Hemostasis. Journal of Thrombosis and Haemostasis. 2024; 22:2081-2092.

Mosley, C; Farrell, CB; Quinn, CT; Shook, LM. A Mixed-Methods Evaluation of a Project ECHO Program for the Evidence-Based Management of Sickle Cell Disease. International Journal of Environmental Research and Public Health. 2024; 21:530.

Mullins, TL K; Mullins, ES. Thrombotic risk associated with gender-affirming hormone therapy. Journal of Thrombosis and Haemostasis. 2024; 22:2129-2139.

Namazzi, R; Bond, C; Conroy, AL; Datta, D; Tagoola, A; Goings, MJ; Jang, JH; Ware, RE; Opoka, R; John, CC. Hydroxyurea reduces infections in children with sickle cell anemia in Uganda. Blood. 2024; 143:1425-1428.

Pabinger, I; Ayash-Rashkovsky, M; Escobar, M; Konkle, BA; Mingot-Castellano, ME; Mullins, ES; Negrier, C; Pan, L; Rajavel, K; Yan, B; Chapin, J. Multicenter assessment and longitudinal study of the prevalence of antibodies and related adaptive immune responses to AAV in adult males with hemophilia. Gene Therapy (Basingstoke). 2024; 31:273-284.

Power-Hays, A; Dong, M; Punt, N; Mizuno, T; Smart, LR; Vinks, AA; Ware, RE. Rationale, Development, and Validation of HdxSim, a Clinical Decision Support Tool for Model-Informed Precision Dosing of Hydroxyurea for Children with Sickle Cell Anemia. Clinical Pharmacology and Therapeutics. 2024; 116:670-677.

Power-Hays, A; Tomlinson, GA; Tshilolo, L; Santos, B; Williams, TN; Olupot-Olupot, P; Smart, LR; Aygun, B; Lane, A; Stuber, SE; Latham, T; Ware, RE. Reducing transfusion utilization for children with sickle cell anemia in sub-Saharan Africa with hydroxyurea: Analysis from the phase I/II REACH trial. American Journal of Hematology. 2024; 99:625-632.

Ricci, K. Medical Therapeutics for the Treatment of Vascular Anomalies: Part 3. Oral and Maxillofacial Surgery Clinics of North America. 2024; 36:125-136.

Sadaf, A; Dong, M; Pfeiffer, A; Korpik, J; Kalfa, TA; Latham, T; Vinks, AA; Ware, RE; Quinn, CT. A pharmacokinetic-pharmacodynamic analysis of l-glutamine for the treatment of sickle cell disease: Implications for understanding the mechanism of action and evaluating response to therapy. British Journal of Haematology. 2024; 205:1147-1158.

Sadaf, A; Dong, M; Pfeiffer, A; Latham, T; Kalfa, T; Vinks, AA; Ware, RE; Quinn, CT. A Population Pharmacokinetic Analysis of L-Glutamine Exposure in Patients with Sickle Cell Disease: Evaluation of Dose and Food Effects. Clinical Pharmacokinetics. 2024; 63:357-365.

Saraf, SL; Hagar, R; Idowu, M; Osunkwo, I; Cruz, K; Kuypers, FA; Brown, RC; Geib, J; Ribadeneira, M; Schroeder, P; Wu, E; Forsyth, S; Kelly, PF; Kalfa, TA; Telen, MJ. Multicenter, phase 1 study of etavopivat (FT-4202) treatment for up to 12 weeks in patients with sickle cell disease. Blood Advances. 2024; 8:4459-4475.

Segbefia, C; Luchtman-Jones, L. Seeing haemoglobin SC: Challenging the misperceptions. British Journal of Haematology. 2024; 205:404-405.

Sekyonda, Z; An, R; Goreke, U; Man, Y; Monchamp, K; Bode, A; Zhang, Q; El-Gammal, Y; Kityo, C; Kalfa, TA; Akkus, O; Gurkan, UA. Rapid measurement of hemoglobin-oxygen dissociation by leveraging Bohr effect and Soret band bathochromic shift. The Analyst. 2024; 149:2561-2572.

Shook, LM; Crosby, LE; Farrell, CB; Nelson, SC. A health equity ECHO for clinicians of individuals with SCD. 2024; 1.

Shook, LM; Rosen, BL; Mara, CA; Mosley, C; Thompson, AA; Smith-Whitley, K; Schwartz, L; Barriteau, C; King, A; Oke, E; Jallow, F; Murphy, B; Crosby, L. Attitudes, Beliefs, and Intention to Receive a COVID-19 Vaccine for Pediatric Patients With Sickle Cell Disease. Journal of Pediatric Hematology/Oncology. 2024; 46:e305-e312.

Shook, LM; Ware, RE. Screening for haemoglobin disorders: One size may not fit all. British Journal of Haematology. 2024; 204:26-28.

Siegert, TF; Opoka, RO; Nakafeero, M; Carman, A; Mellencamp, KA; Latham, T; Hume, H; Lane, A; Ware, RE; Ssenkusu, JM; John, CC; Conroy, AL. Angiopoietin-2 is associated with sickle cell complications, including stroke risk, and decreases with hydroxyurea therapy. 2024; 1:100001.

Unaka, N; Kahn, RS; Spitznagel, T; Henize, AW; Carlson, D; Michael, J; Quinonez, E; Anderson, J; Beck, AF; Alexander, CE; Lamy, M; Power-Hays, A; Quinn, CT; Niss, OY. An Institutional Approach to Equity and Improvement in Child Health Outcomes. Pediatrics. 2024; 154:e2023064994.

Ware, RE; Quinn, CT. The bold promise of gene therapy for sickle cell disease. British Journal of Haematology. 2024; 204:381-382.