Clinical Trials / Research Studies

Clinical Trials / Research Studies

What will happen in the study?

In these studies, children who are eligible to participant will start their growth hormone treatment through the study and be required to attend on-site study visits about every 3 months. Each visit lasts about 2-3 hours on average.

In the first year of the study, children are assigned either the FDA approved daily growth hormone medication or the study medication (once weekly long-acting growth hormone medication). After a period of one year in the study, all children taking the daily growth hormone medication will start taking the once weekly long-acting medication.

Participants will:

• Have blood drawn at multiple visits (some of them will require fasting).
• Have height, weight, body composition and vital signs (blood pressure, breathing rate, heart rate) taken.
• Have physical exams performed by the study doctor (some will include an exam to check for signs of puberty).
• Have electrocardiograms (ECG) or echocardiograms (TTE) performed at some of the visits depending on your diagnosis.
• Have x-rays taken of their hand.
• Be trained on the use and care of the study medication (daily or weekly).
• Be required to log their daily or weekly injections into a study app on a cell phone
• Complete study questionnaires.

Families interested in having their child participate will be given a consent form that thoroughly explains all of the details of the study. A member of the study staff will review the consent form with you and will be sure that all of your questions are answered at the first study visit.