Susceptibility to BK polyomavirus-associated hemorrhagic cystitis in children undergoing allogeneic transplant. Haematologica: the hematology journal. 2025; 110:527-531.
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. Bkpyv Replication Kinetics and Association with Hemorrhagic Cystitis in Pediatric HSCT Recipients. Transplantation and Cellular Therapy.Smoking-Associated Carcinogen-Induced Inflammation Promotes Lung Carcinogenesis via IRAK4 Activation. Clinical Cancer Research. 2025; 31:746-755.
.Clinical spectrum of primary hemophagocytic lymphohistiocytosis: experience of reference centers in Central and Southeast Anatolia. Annals of Hematology. 2025; 104:123-130.
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. Hematopoietic Cell Transplantation for Wiskott-Aldrich Syndrome - Impact of Age, Donor, and Infection: A Pidtc Report. Transplantation and Cellular Therapy.RAS Pathway Mutations and Therapeutics in Vascular Anomalies. Pediatric Blood and Cancer. 2025; 72:e31605.
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. Hydroxyurea to decrease stroke risk in children with sickle cell anemia: a systematic review and meta-analysis.Treatment of focal anaplastic Wilms tumor: A report from the Children's Oncology Group AREN0321 and AREN03B2 studies. Cancer. 2025; 131:e35713.
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. A 10-Year History of Graft Failure in Pediatric Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy.2025; 31:s149-s150.
. Frequent Pulmonary Complications after Allogeneic Hematopoietic Stem Cell Transplant: A Brief Transpire Report. Transplantation and Cellular Therapy.2025; 31:s147.
. Male Gender and Underlying Diagnosis Predisposes to Increased HLA Antibody Burden in Children before Allogeneic Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy.Immunogenicity and Reactogenicity of High- or Standard-Dose Influenza Vaccine in a Second Consecutive Influenza Season. The Journal of Infectious Diseases. 2025; 231:e123-e131.
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. Impact of Graft Versus Host Disease Following Allogeneic Hematopoietic Cell Transplantation on Leukemia Free Survival in Hematologic Malignancies: A CIBMTR Analysis. Transplantation and Cellular Therapy.A Single-Cell Transcriptome Atlas of Epithelial Subpopulations in HPV-Positive and HPV-Negative Head and Neck Cancers. Viruses-Basel. 2025; 17:461.
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. Beyond Survival: Assessing Renal and Cardiovascular Health in Fanconi Anemia Adolescents and Young Adults Post-Stem Cell Transplant. Transplantation and Cellular Therapy.2025; 31:s364-s365.
. Real-World Assessment of Patient Adherence to the Late Effects Screening Recommendations Among Hematopoietic Cell Transplantation Survivors. Transplantation and Cellular Therapy.The Fas-mediated apoptosis assay: From concept to clinical application. Journal of Immunological Methods. 2025; 537:113812.
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. 633. Incidence and Outcomes of Pediatric Allogeneic Hematopoietic Cell Transplant (allo-HCT) Recipients Under Surveillance and Not Under Surveillance for Human Adenovirus (HAdV) in the Post-HCT Period. Open Forum Infectious Diseases.2025; 31:s145-s146.
. Differential Filtration of Macromolecules: A Novel Indicator of Mortality Risk in Pediatric HSCT Patients. Transplantation and Cellular Therapy.Reducing clinical trial eligibility barriers for patients with MDS: an icMDS position statement. Blood. 2025; 145:1369-1381.
.Multiomics dissection of human RAG deficiency reveals distinctive patterns of immune dysregulation but a common inflammatory signature. Science immunology. 2025; 10:eadq1697.
.Three-generation female cohort with macrocytic anemia and iron overload. American Journal of Hematology. 2025; 100:133-138.
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. 1187: ECMO IN PEDIATRIC ONCOLOGIC AND HEMATOPOIETIC STEM CELL TRANSPLANT PATIENTS: A COMPARATIVE ANALYSIS. Critical Care Medicine.Vascular network-inspired diffusible scaffolds for engineering functional midbrain organoids. Cell Stem Cell. 2025; 32:824-837.e5.
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. Abstract 1596: Tumor-derived RAC1A159V gain-of-function mutation promotes an immunosuppressive tumor microenvironment and represses response to immune checkpoint inhibitors. Cancer Research.2025; 145:e29.
. 118: Randomized, Double-Blind, Phase 2 Study of Alpelisib in Pediatric and Adult Patients With PIK3CA-Related Overgrowth Spectrum (PROS). Journal of Investigative Dermatology.Prothrombin prevents fatal T cell-dependent anemia during chronic virus infection of mice. JCI insight. 2025; 10:e181063.
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. Perioperative Management with Efanesoctocog Alfa in Adults, Adolescents, and Children with Severe Hemophilia A in the Phase 3 XTEND Clinical Program. Hamostaseologie.Emapalumab Treatment in Patients With Rheumatologic Disease-Associated Hemophagocytic Lymphohistiocytosis in the United States: A Retrospective Medical Chart Review Study. Arthritis and Rheumatology. 2025; 77:226-238.
.YTHDF2 promotes ATP synthesis and immune evasion in B cell malignancies. Cell. 2025; 188:331-351.e30.
.An engineered β-globin homology donor reveals insights into β-globin expression and betters HDR. Molecular Therapy. 2025; 33:1308-1309.
.Protein-Protein Interactions of Odorant and G Protein-Coupled Receptors: A BRET Analysis Approach. Methods in molecular biology (Clifton, N.J.). 2025; 2915:161-168.
.Yellow Fluorescent Protein Quenching Assay for Analyzing Odorant Receptor Activity. Methods in molecular biology (Clifton, N.J.). 2025; 2915:169-177.
.Associations Between Pain Scores and Opioid Doses With Emergency Department Disposition and Return Visit Rates in Children With Sickle Cell Disease. Pediatric Blood and Cancer. 2025; e31750.
.Oxidative Stress Early After Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:135.e1-135.e10.
.Globalization in clinical drug development for sickle cell disease. American Journal of Hematology. 2025; 100:4-9.
."From Drowning to Treading Water ": Adolescents and Young Adults Living with Incurable and Indolent Metastatic Soft Tissue Sarcoma for More than Two Years. Cancers. 2025; 17:442.
.Engraft: A Collaborative Learning Health Network for Enhanced Transplant and Cellular Therapy Outcomes. Transplantation and Cellular Therapy. 2025; 31:123-134.
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. Gene Therapy with Reduced-Intensity Conditioning for Sickle Cell Disease. Transplantation and Cellular Therapy.2025; 53.
. 667: SEVERE METHOTREXATE-INDUCED NEUROTOXICITY IN A HISPANIC ADOLESCENT GIRL WITH B-ALL. Critical Care Medicine.Hydroxyurea for Children and Adults with Hemoglobin SC Disease. 2025; 4:EVIDoa2400402.
.A Phase 1/2 Study of Lenvatinib in Combination With Everolimus in Recurrent and Refractory Pediatric and Young Adult Solid Tumors. Pediatric Blood and Cancer. 2025; e31692.
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. Outcome Analysis Post Virus-Specific T Cell Therapy for the Treatment of Adenoviremia in Immunocompromised Pediatric Patients. Transplantation and Cellular Therapy.Relevance of Recent Thymic Emigrants Following Allogeneic Hematopoietic Cell Transplantation for Pediatric Patients with Inborn Errors of Immunity. Transplantation and Cellular Therapy. 2025; 31:265.e1-265.e12.
.Reconstitution of Norovirus-Specific T-Cell Responses Following Hematopoietic Stem Cell Transplantation in Patients With Inborn Errors of Immunity and Chronic Norovirus Infection. The Journal of Infectious Diseases. 2025; 231:773-783.
.Comment on: "Comment on: Bivalirudin During Thrombolysis With Catheter-Directed tPA in a Heparin-Refractory Patient: A Case Report ": The Promise of Dilute Thrombin Time and Drug-Calibrated Assays for Improved Bivalirudin Monitoring. Pediatric Blood and Cancer. 2025; 72:e31418.
.Roadmap to a Global Template for Implementation of Ototoxicity Management for Cancer Treatment. Ear and Hearing. 2025; 46:286-297.
.Dopaminergic encoding of future defensive actions in the mouse nucleus accumbens. Editor, Bahar I. PNAS Nexus. 2025; 4:pgaf128.
.DNAJB1-PKAc Kinase Is Expressed in Young Patients with Pediatric Liver Cancers and Enhances Carcinogenic Pathways. Cancers. 2025; 17:83.
.Feasibility and Safety of Intratympanic Administration of Sustained-Exposure Dexamethasone Thermosensitive Gel (OTO-104) for Prevention of Cisplatin-Induced Hearing Loss in Children: A Multisite Phase 2 Randomized Clinical Trial. Pediatric Blood and Cancer. 2025; 72:e31680.
.Rhabdoid Tumor of the Kidney and Soft Tissues: Results from National Wilms Tumor Study-5 and Children's Oncology Group Study AREN0321. Pediatric Blood and Cancer. 2025; 72:e31490.
.A novel POT1-TPD presentation: A germline pathogenic POT1 variant discovered in a patient with newly diagnosed posterior fossa ependymoma. Cancer genetics. 2025; 292-293:38-43.
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. Understanding Diversity: An ASTCT-NMDP Access Initiative Survey of the Hematopoietic Cell Transplant and Cellular Therapy Nonphysician Workforce. Transplantation and Cellular Therapy.2025; 31:s361.
. Physician Workforce Diversity in the Hematopoietic Cell Transplant and Cellular Therapy Ecosystem: An ASTCT-NMDP Access Initiative Survey. Transplantation and Cellular Therapy.Cellular taxonomy of the preleukemic bone marrow niche of acute myeloid leukemia. Leukemia. 2025; 39:51-63.
.Duration of anticoagulation for venous thromboembolism in pediatric patients: Evaluation of the Duration of Therapy for Thrombosis in Children (Kids-DOTT) trial outcomes at 2 years. Journal of Thrombosis and Haemostasis. 2025; 23:651-656.
.Examining the role of the photopigment melanopsin in the striatal dopamine response to light. Frontiers in Systems Neuroscience. 2025; 19:1568878.
.Shining a TORCH on a Case of Blueberry Muffin Rash in a Newborn Infant. NeoReviews.org. 2025; 26:e191-e196.
.An inflammatory state defines a high-risk T-lineage acute lymphoblastic leukemia subgroup. Science Translational Medicine. 2025; 17:eadr2012.
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. DARA to Believe: Anti-CD38 Antibody Improves Outcomes in Relapsed/Refractory Pediatric T-Cell Lymphoblastic Leukemia and Lymphoma.2025; 31:s153.
. Managing Diffuse Alveolar Hemorrhage in Pediatric HSCT with Inhaled and Intrabronchial Therapy: A Case Series of Targeted Hemostatic Intervention. Transplantation and Cellular Therapy.Reply to: Comment on Anemia in Young Children and the Association With Socioeconomic Deprivation Indices. Pediatric Blood and Cancer. 2025; e31743.
.Anemia in Young Children and the Association With Socioeconomic Deprivation Indices. Pediatric Blood and Cancer. 2025; e31663.
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. Incidence of Transplant-Associated Thrombotic Microangiopathy (TA-TMA) Is Not Lowered By Reduction of Acute GvHD (aGvHD) in Patients Receiving Post-Transplant Cyclophosphamide (PTCy) GvHD Prophylaxis: A Report from the MIDAS (Microangiopathy, Endothelial Damage in Adults undergoing Stem cell transplantation) Consortium. Transplantation and Cellular Therapy.Impact of Hepatoblastoma on Infectious Complications Following Pediatric Liver Transplantation. Pediatric Transplantation. 2025; 29:e70035.
.Causes and Consequences of Persistent Anemia after 6 Months of Antiretroviral Therapy in Tanzania: An Observational Comparative Cohort Study. American Journal of Tropical Medicine and Hygiene. 2025; 112:234-241.
.GPR68 supports AML cells through the calcium/calcineurin pro-survival pathway and confers chemoresistance by mediating glucose metabolic symbiosis. Biochimica et Biophysica Acta (BBA): Molecular Basis of Disease. 2025; 1871:167565.
.Engaging Parents of Children With Sickle Cell Disease in Shared Decision-Making for Hydroxyurea: The ENGAGE-HU Study. Pediatric Blood and Cancer. 2025; 72:e31639.
.IRAK1/4/pan-FLT3 Kinase Inhibitors with Reduced hERG Block as Treatments for Acute Myeloid Leukemia. ACS Medicinal Chemistry Letters. 2025; 16:887-895.
.Neutrophil-derived vesicles control complement activation to facilitate inflammation resolution. Cell. 2025; 188:1623-1641.e26.
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. Establishing the Engraft Multi-Center Tri-Use Registry. Transplantation and Cellular Therapy.2025; 31:s98.
. Longitudinal Outcomes of Fertility Potential in Female Pediatric and Young Adult Allogeneic Hematopoietic Stem Cell Transplant Survivors. Transplantation and Cellular Therapy.2025; 31:s93-s94.
. Acute Toxicities and Early Outcomes of Tandem Autologous Stem Cell Transplantation in Pediatric High-Risk Neuroblastoma: A Multicenter Study. Transplantation and Cellular Therapy.Chronic Graft-Versus-Host Disease Adversely Impacts School Performance in Children and Young Adults. Transplantation and Cellular Therapy. 2025; 31:99.e1-99.e11.
.Stretchable Heat Transfer Eco-Materials: Mesogen Grafted NR-Based Nanocomposites with High Thermal Conductivity and Low Dielectric Constant. Small. 2025; 21:e2406066.
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. Single Center Experience of Belumosudil in Children < 12 Years, Adolescents and Young Adults. Transplantation and Cellular Therapy.2025; 2:100055.
. Kinetics of DNases after hematopoietic stem cell transplant.Ubiquitin-conjugating enzyme UBE2N modulates proteostasis in immunoproteasome-positive acute myeloid leukemia. The Journal of Clinical Investigation. 2025; 135.
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. Translating biomarker insights into practice: a path forward in TA-TMA management. Frontiers in Medicine.Pediatric Transplant and Cellular Therapy Consortium RESILIENT Conference on Pediatric Chronic Graft-versus-Host Disease Survivorship after Hematopoietic Cell Transplantation: Part III. Long-Term Impact of Chronic Graft-versus-Host Disease on Endocrinologic, Cardiovascular, and Metabolic Outcomes in Survivors of Pediatric Hematopoietic Cell Transplantation. Transplantation and Cellular Therapy. 2025; 31:297.e1-297.e15.
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. Addition of Thiotepa to Alemtuzumab, Fludarabine, and Melphalan Reduced-Intensity Conditioning Reduces Secondary Graft Failure in Allogeneic HSCT for Inborn Errors of Immunity.Germline DDX41 mutations in myeloid neoplasms: the current clinical and molecular understanding. Current Opinion in Hematology. 2025; 32:67-76.
.Systematic Review of Pain Assessment Measures Used in Pediatric Acute Lymphoblastic Leukemia. Psycho-Oncology: journal of the psychological, social and behavioral dimensions of cancer. 2025; 34:e70063.
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. Pravastatin Prophylaxis Is Safe and Feasible in Children and Young Adults Undergoing Allogeneic HSCT: A Prospective, Single Arm Cohort Study. Transplantation and Cellular Therapy.2025; 31:s311-s312.
. Beyond Graft-Vs-Host Disease: The Role of Cellular Senescence in Persistent Liver Injury in Fanconi Anemia after HSCT. Transplantation and Cellular Therapy.2025; 31:s137.
. The Tell-Tale Heart: A Cytokine Storm Story of Pericardial Effusions after HSCT. Transplantation and Cellular Therapy.2025; 31:s308-s309.
. Transcriptomic Alterations and Clonal Evolution Identifies a Pre-Emptive Indication for Hematopoietic Stem Cell Transplant in Fanconi Anemia. Transplantation and Cellular Therapy.Prevalence of cytopenia(s) and somatic variants in patients with DDX41 mutant germline predisposition syndrome. British Journal of Haematology. 2025; 206:1109-1120.
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. Higher Dose Intravenous Posaconazole Is Safe and Necessary for Achievement of Therapeutic Targets and Prevention of Infections in Pediatric Hematopoietic Stem Cell Transplant Patients. Transplantation and Cellular Therapy.2025.
. Medulloblastoma of early childhood. Salvage and outcome after initial CSI sparing approaches.Clinical Characteristics and Outcomes of Central Nervous System Tumors Harboring NTRK Gene Fusions. Clinical Cancer Research. 2025; 31:561-572.
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. Urine Kidney Injury Biomarkers Predict TMA Risk in Pediatric HSCT Recipients. Transplantation and Cellular Therapy.2025; 31:s313-s314.
. Supar Is a Novel and Powerful Biomarker of TMA and Kidney Injury after HSCT. Transplantation and Cellular Therapy.SUV39H1 maintains cancer stem cell chromatin state and properties in glioblastoma. JCI insight. 2025; 10:e186344.
.Loss of Cpt1a results in elevated glucose-fueled mitochondrial oxidative phosphorylation and defective hematopoietic stem cells. The Journal of Clinical Investigation. 2025; 135:e184069.
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. Effect of Clinically Relevant Immunosuppressants on Viral Specific T-Cell (VST) in Vitro Function. Transplantation and Cellular Therapy.Fusion-specific chromatin profiles mediate transcriptional heterogeneity in MLL-rearranged acute lymphoblastic leukemia. Blood Advances. 2025; 9:856-861.
.Structural Dynamics of Rho GTPases. Journal of Molecular Biology. 2025; 437:168919.
.Improving Time to Bleeding Disorder Treatment in the Emergency Department. Pediatric Blood and Cancer. 2025; 72:e31570.
.PBAE-PEG-based lipid nanoparticles for lung cell-specific gene delivery. Molecular Therapy. 2025; 33:1154-1165.
.The role of oligodendrocyte progenitor cells in the spatiotemporal vascularization of the human and mouse neocortex. Glia. 2025; 73:140-158.
.Clinical, Immunologic, and Genetic Characteristics in Patients With Syndrome of Undifferentiated Recurrent Fevers. Arthritis and Rheumatology. 2025; 77:596-605.
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. Establishing a Quality Improvement Education Platform in the Engraft Learning Network. Transplantation and Cellular Therapy.2025; 31:s145.
. The HCT Protein Shake: Moderate and Severe Proteinuria Are Specific to TA-TMA. Transplantation and Cellular Therapy.2025; 12:ofae631.310.
. P-103. Adenoviremia Clearance Following Treatment with Intravenous (IV) Brincidofovir (BCV) in Immunocompromised Patients is Associated with Positive Clinical Disease Response: Preliminary Outcomes from the ATHENA Phase IIa Study. Open Forum Infectious Diseases.2025; 1.
. Precision Alemtuzumab Dosing Results in Day 0 Target Range Achievement in 80% of IEI Patients and Minimizes Risks of GVHD, Clinically Significant Mixed Chimerism, and Secondary Graft Failure.Diagnostic testing for hemophagocytic lymphohistiocytosis. Journal of Immunological Methods. 2025; 537:113816.
.Allogeneic haematopoietic stem-cell transplantation for children with refractory systemic juvenile idiopathic arthritis and associated lung disease: outcomes from an international, retrospective cohort study. The Lancet. Rheumatology. 2025; 7:e243-e251.
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. The First Prospective Screening Study of BK Polyomavirus (BKPyV) Hemorrhagic Cystitis after HSCT. Transplantation and Cellular Therapy.2025; 31:s317-s318.
. Defining and Assessing Poor Graft Function after Allogeneic HSCT in Children and Young Adults. Transplantation and Cellular Therapy.2025; 31:s514-s515.
. Plasma LILRA6 Levels Influence BK Polyomavirus Cystitis after HSCT. Transplantation and Cellular Therapy.Developing Behavior Change Model-Informed and Participant-Engaged Retention Strategies for Adolescents and Young Adults With Cancer Enrolled on Behavioral and/or Psychosocial Trials. Pediatric Blood and Cancer. 2025; 72:e31583.
.Phase 1 study of quercetin, a natural antioxidant for children and young adults with Fanconi anemia. Blood Advances. 2025; 9:1927-1939.
.Emapalumab for the Treatment of Immune-Mediated Graft Failure after HSCT. Bone Marrow Transplantation. 2025; 60:406-411.
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. Nurse Driven Central Line Rounding Utilized to Improve Bone Marrow Transplant Patient Outcomes: An Update. Transplantation and Cellular Therapy.Tunneling nanotube-like structures regulate distant cellular interactions during heart formation. Science. 2025; 387:eadd3417.
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. Unraveling the Challenges of Non-Responders to the Eculizumab Treatment with High-Risk Hematopoietic Stem Cell Transplant-Associated Thrombotic Microangiopathy (TA-TMA). Transplantation and Cellular Therapy.2025; 13:11-16.
. Quality of Life for Rural and Appalachian Pediatric Brain Tumor Survivors in Ohio and Kentucky. Clinical Practice in Pediatric Psychology.Receipt of Fluoroquinolone Prophylaxis is not Associated With Development of Vancomycin-Resistant Enterococcus Colonization During Pediatric Hematopoietic Cell Transplantation. Journal of the Pediatric Infectious Diseases Society. 2025; 14:piaf010.
.Clinical Use of ZSCAN4 for Telomere Elongation in Hematopoietic Stem Cells. 2025; 4:EVIDoa2400252.
.G-CSF resistance of ELANE-mutant neutropenia depends on SERF1-containing truncated-neutrophil elastase aggregates. The Journal of Clinical Investigation. 2025; 135:e177342.
.Perspectives on the current diagnostic and treatment paradigms in secondary hemophagocytic lymphohistiocytosis (HLH). Orphanet Journal of Rare Diseases. 2025; 20:200.
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. Soluble Fms-like Tyrosine Kinase-1 (sFlt-1) As a Clinical Biomarker for Individual Susceptibility to Post-Transplant Complications: A Report from the MIDAS Consortium. Transplantation and Cellular Therapy.Acute Toxicities of Proton Craniospinal Irradiation in Pediatric Medulloblastoma: A Pediatric Proton/Photon Consortium Registry (PPCR) Study. International Journal of Particle Therapy. 2025; 16:100747.
.Stroke prevention in Hispanic children with sickle cell anemia: the SACRED trial. Blood Advances. 2025; 9:1791-1800.
.Unraveling lipid metabolism for acute myeloid leukemia therapy. Current Opinion in Hematology. 2025; 32:77-86.
.Neurocognitive outcomes and functional independence in adult survivors of childhood medulloblastoma diagnosed over 3 decades. Neuro-Oncology. 2025; 27:254-266.
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. ‘Blin’-ing Is Winning for Children With B-Cell Acute Lymphoblastic Leukemia.2025; 44:s355.
. (750) Single Cell Technology Shines LIGHT on Acute Lung Allograft Dysfunction. The Journal of Heart and Lung Transplantation.Pharmacokinetic-Guided Hydroxyurea to Reduce Transfusions in Ugandan Children with Sickle Cell Anemia: Study Design of the Alternative Dosing And Prevention of Transfusions Trial. Acta Haematologica. 2025; 148:208-219.
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. 23P Pre-diagnostic imaging reveals rapid emergence and progression of small cell carcinoma of the ovary hypercalcemic type (SCCOHT): Implications for monitoring carriers of SMARCA4 germline pathogenic variants (GPVs). ESMO Open.Granulocyte-Macrophage Colony Stimulating Factor Receptor Contributes to Plexiform Neurofibroma Initiation. Cancers. 2025; 17:905.
.The modern use of hydroxyurea for children with sickle cell anemia. Haematologica: the hematology journal. 2025; 110:1061-1073.
.The Voxelotor Effect: Decreased Affinity for New Drugs for Sickle Cell Disease?. Pediatric Blood and Cancer. 2025; 72:e31475.
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. Perception and Reality of Racial and Ethnic Workforce Diversity in the U.S HCT/CT Workforce: Results from the ASTCT-NMDP Access Initiative Survey. Transplantation and Cellular Therapy.2025; 31:s25-s26.
. Pre-Transplant Complement Activation and Transplant-Associated Thrombotic Microangiopathy (TA-TMA) across Diagnostic Groups. Transplantation and Cellular Therapy.Isotretinoin has no effect on event-free survival across high-risk medulloblastoma molecular groups when added to maintenance: A secondary analysis of the Children's Oncology Group ACNS0332 data. Neuro-Oncology Advances. 2025; 7:vdaf054.
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. 137 Schwann Cell Glial Cell Line-Derived Neurotrophic Factor Signaling Influences Pain in Neurofibromatosis 1. Journal of Pain.Long-term kidney outcomes in survivors of Wilms tumor: a single-center retrospective cohort study. Pediatric Nephrology. 2025; 40:1603-1611.
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. 44: Capillary Malformation-Arteriovenous Malformation Syndrome: Proposed Consensus Guidelines. Journal of Investigative Dermatology.Validation of Pediatric Self-Report Pain Scales in Sub-Saharan Africa: A Systematic Review. Journal of Pain and Symptom Management. 2025; 69:e103-e112.
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. Kymriah Real-World Effectiveness and Functional Persistence in Acute Lymphoblastic Leukemia (ALL) (KareALL): A Retrospective Analysis of the Effect of Current Tisagenlecleucel (tisa-cel) Manufacturing in Pediatric and Young Adult Patients (pts) with ALL. Transplantation and Cellular Therapy.2025; 31:s133.
. TA-TMA Evolution and Individual Susceptibility at the Proteome Level. Transplantation and Cellular Therapy.2025; 31:s535-s536.
. Variation in Central Venous Catheter Practices and Complications after Stem Cell Transplant: A Multi-Center Survey of the Engraft Learning Network. Transplantation and Cellular Therapy.2025; 85:3155.
. Abstract 3155: High-throughput drug repositioning identifies dinaciclib as a potent osteosarcoma inhibitor. Cancer Research.Clinical Utility of the Addition of Molecular Genetic Testing to Newborn Screening for Hemoglobinopathies for Confirmation of Alpha-Thalassemia Trait. International Journal of Neonatal Screening. 2025; 11:12.
. .Preclinical efficacy of a modified gamma-globin lentivirus gene therapy in Berkeley sickle cell anemia mice and human xenograft models. Molecular Therapy-Methods & Clinical Development. 2025; 33:101439.
.Sociodemographic Characteristics of Patients Seen at Vascular Anomaly Centers in the United States. Pediatric Blood and Cancer. 2025; 72:e31661.
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. Pre-Transplant Endothelial Activation May Increase Individual Susceptibility Transplant-Associated Thrombotic Microangiopathy in Adults: A Report from the MIDAS Consortium. Transplantation and Cellular Therapy.2025; 31:s489.
. Scrubbing Olympics: Next Steps. Transplantation and Cellular Therapy.2025; 31:s167.
. The Novel Role of Pilra in BK Polyomavirus Cystitis after HSCT. Transplantation and Cellular Therapy.2025; 31:s146.
. Inbody Assessments Reveal Important Changes in Body Mass Composition during HCT. Transplantation and Cellular Therapy.The Adverse Event Landscape of Stem Cell Transplant: Evidence for AGVHD Driving Early Transplant Associated Toxicities. Transplantation and Cellular Therapy. 2025; 31:109.e1-109.e13.
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. The Role of Second Hematopoietic Cell Transplantation (HCT2) in Patients with Severe Combined Immunodeficiency (SCID): A Report from the Primary Immune Deficiency Treatment Consortium (PIDTC). Transplantation and Cellular Therapy.Hemostatic derangements associated with cardiopulmonary bypass predict outcomes in pediatric patients undergoing corrective heart surgery. Journal of Thrombosis and Haemostasis. 2025; 23:492-503.
.Characteristics of patients with liver tumors deemed ineligible for enrollment on Children's Oncology Group trial AHEP1531: An opportunity to expand inclusion criteria and improve outcome. Pediatric Blood and Cancer. 2025; 72:e31389.
.Modelling a pathological GSX2 variant that selectively alters DNA binding reveals hypomorphic mouse brain defects. DMM Disease Models and Mechanisms. 2025; 18:dmm052110.
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. Pre-HCT Creatinine and Early Post-HCT Changes in Creatinine and Blood Pressure Associate with Severe Transplant Associated Thrombotic Microangiopathy (TA-TMA): A Report from the MIDAS (Microangiopathy, Endothelial Damage in Adults undergoing Stem cell transplantation) Consortium. Transplantation and Cellular Therapy.Splicing regulatory dynamics for precision analysis and treatment of heterogeneous leukemias. Science Translational Medicine. 2025; 17:eadr1471.
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. Characterizing the Gut Microbiome in Pediatric Patients Undergoing Hematopoietic Cell Transplant for a Non-Malignant Diagnosis. Transplantation and Cellular Therapy.2025; 31:s355.
. Influence of the Incorporation of a Muslim Chaplain on Medical Decision-Making in a Pediatric Hematopoietic Cell Transplant Program. Transplantation and Cellular Therapy.Regulated GATA1 expression as a universal gene therapy for Diamond-Blackfan anemia. Cell Stem Cell. 2025; 32:38-52.e6.
.Management, Trends, and Recommendations for Intra-abdominal Lymphatic Malformations: A Single-Center Retrospective Review. Journal of Pediatric Surgery. 2025; 60:162223.
.Using cancer phenotype sex-specificity to enable unbiased penetrance estimation of SMARCA4 pathogenic variants for small cell carcinoma of the ovary, hypercalcemic type (SCCOHT). Genetics in Medicine. 2025; 27:101287.
.TIFAB modulates metabolic pathways in KMT2A::MLLT3-induced AML through HNF4A. Blood Advances. 2025; 9:844-855.
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. Single Cell Rnaseq Identifies Novel Graft Rejection Mechanisms and Resurgence of Recipient NK and T-Cells. Transplantation and Cellular Therapy.Differential regulation of fetal bone marrow and liver hematopoiesis by yolk-sac-derived myeloid cells. Nature Communications. 2025; 16:4427.
.Secondary Anticoagulation Use in Patients < 21 Years Old following Primary Anticoagulant Treatment for Provoked Venous Thromboembolism: Findings from the Kids-DOTT Trial. Seminars in Thrombosis and Hemostasis. 2025; 51:343-347.
.Intercellular mRNA transfer alters the human pluripotent stem cell state. Proceedings of the National Academy of Sciences of USA. 2025; 122:e2413351122.
.The Functional Characterization of Venous Thromboembolic Disease (FUVID) study: rationale, design, and methods of a prospective, observational, multicenter study to evaluate mechanisms of exercise intolerance and dyspnea following pediatric pulmonary embolism. Research and Practice in Thrombosis and Haemostasis. 2025; 9:102669.
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. First Relapse, Second Chance: Determinants of Survival After First Relapse in Pediatric Acute Lymphoblastic Leukemia.