High-dose chemotherapy and re-irradiation associated with improved overall survival in patients with relapsed central nervous system (CNS) non-germinomatous germ cell tumors (NGGCT). Clinical Oncology. 2026; 57:104278.
Marrow-ablative chemotherapy and re-irradiation are associated with improved overall survival in patients with relapsed central nervous system nongerminomatous germ cell tumors. Journal of Neuro-Oncology. 2026; 177(3).
Comparison of Fludarabine Versus Bendamustine as a Lymphodepleting Chemotherapy Prior to CAR-T for Large Cell Lymphoma. Transplantation and Cellular Therapy. 2026.
Liberalizing hospital proximity requirements for children/young adults with low-burden B-ALL receiving tisagenlecleucel. Blood advances. 2026; 10(1):106-110.
Neurofibromatosis type 1-plexiform neurofibromas: Integrating treatment across pediatric and adult populations. Neuro-Oncology. 2026; 28(4):847-863.
Long-term Ocular Safety in Children Treated with Mitogen-Activated Protein Kinase Pathway Inhibitor Therapy. Ophthalmology (Rochester, Minn.). 2026; 133(2):291-294.
Engineering functionality-optimized fully human B7-H3 CAR T cells for enhanced solid tumor therapy. Cell Reports Medicine. 2026; 7(5):102782.
Global variability in cardiovascular care of pediatric cancer patients and survivors: survey results from the International Cardio Oncology Society (ICOS) Cardio-Oncology. 2026.
Levetiracetam therapeutically targets GABAergic synapses in diffuse midline glioma. Nature Medicine. 2026; 32(10):3792-3800.
CPX-351 in High-Risk Relapsed Pediatric Acute Leukemia: Real-World Phase 1 Data Establishing the FDA-Approved Dose. Pediatric Blood and Cancer. 2026; 73(6):e70268.
Safety and pharmacokinetics (PK) of lurbinectedin (lurbi) in pediatric patients (pts) with relapsed/refractory (R/R) solid tumors and preliminary antitumor activity in pediatric and young adult pts with R/R Ewing sarcoma (EwS): Results from a phase 1 study. Journal of Clinical Oncology. 2026; 44(16_suppl):11518-11518.
EP074 / #800 SINGLE-CELL EVIDENCE OF LATE KIDNEY INJURY AFTER PROTON BEAM THERAPY DESPITE PRESERVED RENAL FUNCTION. International Journal of Particle Therapy. 2026; 21:101399.
Rare cancers research: Current state of knowledge and emerging opportunities for prevention and interception. Journal of the National Cancer Institute. 2026.
P-522. Epidemiology of respiratory viral infections in pediatric acute leukemia patients. Open Forum Infectious Diseases. 2026; 13(Supplement_1):ofaf695.737.
Boosting the Predictive Power of Virus-Specific T-Cell Clinical Trials via Generative Models. Computational and Structural Biotechnology Journal. 2026; 35(1):0208.
Real-world outcomes of nivolumab-AVD and brentuximab vedotin-AVD in paediatric and adult advanced-stage Hodgkin lymphoma. British Journal of Haematology. 2026.
Cardio-protection and monitoring for early phase clinical trials: Recommendations from the therapeutic advances in childhood leukemia and lymphoma (TACL) consortium. Journal of the National Cancer Institute. 2026.
Social Support and Barriers to Medication Adherence Among Adolescents and Young Adults With Cancer. Pediatric Blood and Cancer. 2026; e70723.
Wide Ranging Neurobehavioral Phenotype in Individuals With Costello Syndrome. American Journal of Medical Genetics, Part A. 2026; 200(5):1138-1144.
FAST-02: Results from the second in-human prospective evaluation of single-fraction proton FLASH for symptomatic thoracic bone metastases. Radiotherapy and Oncology. 2026; 222:111671.
Third-Party Viral Specific T Cells for Immunocompromised Hosts and Access Barriers: A Review and Commentary by an Expert Panel from ASTCT. Transplantation and Cellular Therapy. 2026; 32(9):1051.e1-1051.e10.
A CAR-T Tonic Signaling Code Predicts Anti-Tumor Efficacy in Diffuse Midline Glioma. Neuro-Oncology. 2026.
Venetoclax as Salvage Treatment for Relapsed/Refractory B-ALL Post-CAR-T Therapy. Pediatric Blood and Cancer. 2026.
A real-world multi-institution experience of standard versus alternative dosing regimens of inotuzumab ozogamicin for relapsed/refractory paediatric B-cell acute lymphoblastic leukaemia. British Journal of Haematology. 2026.
Age-based pegaspargase dosing is safe and achieves therapeutic levels in infants with ALL: report from COG AALL15P1. Blood advances. 2026; 10(1):70-74.
DNMT3A R882C variant in a patient with a presumed pineal gland tumor, highlighting potential tumor susceptibility in Tatton-Brown-Rahman syndrome. Cancer Genetics. 2026; 302-303:162-165.
Characterization of the clonal hierarchy and immunophenotype of PTPN11 mutations in acute myeloid leukemia. JCI Insight. 2026; 11(4).
Emapalumab for Immune Effector Cell-Associated Hemophagocytic Lymphohistiocytosis-Like Syndrome Following CD19-Directed CAR-T in Two Patients With B-ALL: Clinical and Biomarker Correlates. Pediatric Blood and Cancer. 2026; 73(8):e70406.
Biomarker Elevations Associated with Immune Effector Cell-Associated Hemophagocytic Lymphohistiocytosis-like Syndrome after CD19-Directed CAR-T Therapy in Children and Young Adults with Acute B-Lymphoblastic Leukemia. Transplantation and Cellular Therapy. 2026; 32(2):s177.
DEK Loss Induces Task-specific Deficits in Learning and Memory and Reprograms the Hippocampal Transcriptome in Mice. Molecular Neurobiology. 2026; 63(1).
MEK inhibitor-induced dropped head syndrome in pediatrics. Neuro-Oncology Pediatrics. 2026; 2(2):wuag024.
Malignant peripheral nerve sheath tumor development during MEK inhibitor treatment: A pre-clinical study and a clinical case series. Neuro-Oncology Advances. 2026; 8(1):vdag180.
Bortezomib and vorinostat in combination with mitoxantrone, dexamethasone, and pegasparaginase during induction and reinduction for infants with acute lymphoblastic leukaemia: a multicentre single-arm phase 1/2 study. The Lancet Haematology. 2026; 13(3):e144-e156.
Outcomes of Allogeneic Stem Cell Transplantation In the Adolescent and Young Adult Population with Acute Lymphoblastic Leukemia Based on Transplant Center: A Center for International Blood and Marrow Transplant Research (CIBMTR) Study. Transplantation and Cellular Therapy. 2026; 32(2):s112.
Base-Edited Breakthrough: Universal CD7 Chimeric Antigen Receptor T Cells Rewriting the Playbook for Relapsed T-Cell Acute Lymphoblastic Leukemia. The Hematologist. 2026; 23(3).
ID #112 PAEDNEOVAX - Multicentre, investigator-initiated phase I/II study to assess safety and efficacy of personalised mRNA vaccine targetting tumour-associated neoantigens in children and young adults with high-risk brain tumours. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.021.
Discrepancies between primary and secondary interpretations of pediatric nuclear medicine imaging examinations. Pediatric Radiology. 2026; 56(2):464-472.
Discordant neoplasms in monozygotic twins with a germline RECQL5 variant. Cancer Genetics. 2026; 306-307:232-236.
LONG-TERM CRYOPRESERVATION PRESERVES THE BIOLOGICAL AND MECHANOBIOLOGICAL ACTIVITY OF THIRD-PARTY VIRUS-SPECIFIC T CELLS. Cytotherapy. 2026; 28(5):102608.
Predictive capacity of mismatch repair status in the use of immune checkpoint inhibitors for the treatment of aggressive pituitary tumors and pituitary carcinomas: An illustrative case report and literature review. Surgical Neurology International. 2026; 17:252.
Multi-Institutional Annotated Multiparametric MRI Dataset of Pediatric High-Grade Gliomas. Radiology: Artificial Intelligence. 2026; 8(3):e250902.
Patient-Level Barriers and Facilitators to Inpatient Physical Therapy in Adolescents and Young Adults With a Hematological Malignancy: A Qualitative Study. Pediatric Blood and Cancer. 2026; 73(4):e70129.
Cancer risk in adults with pathogenic germline variants in RAS/MAPK genes using genomic ascertainment. Genetics in Medicine. 2026; 28(6):102561.
SARC031: A Phase II Trial of Selumetinib and Sirolimus for Patients with Unresectable or Metastatic Malignant Peripheral Nerve Sheath Tumors (MPNST). Clinical Cancer Research. 2026; 32(6):1068-1077.
OP191 / #572 PROTON THERAPY ELICITS A UNIQUE TRANSCRIPTOMIC RESPONSE IN ORAL CANCER ORGANOIDS. International Journal of Particle Therapy. 2026; 21:101929.
In vitro determination of patient-specific variation challenges the universal RBE gold standard for proton radiation therapy. Clinical and Translational Radiation Oncology. 2026; 56:101046.
Use of Radiographic Features for Risk Stratification of Ovarian Masses in Children and Adolescents. Journal of Surgical Research. 2026; 326:507-517.
Pain Experiences During Early Treatment for Pediatric Acute Lymphoblastic Leukemia: A Qualitative Study. Psycho-Oncology. 2026; 35(7):e70550.
Pain, Internalizing Symptoms, Posttraumatic Stress, and Alcohol Use Among Young Adult Survivors of Cancer. Pediatric Blood and Cancer. 2026; 73(4):e70154.
Acute kidney injury during treatment of pediatric brain tumors: a retrospective analysis of survivors. Pediatric Research. 2026.
Tempered optimism: Advances in the precision medicine era for pediatric low-grade glioma. Neuro-Oncology. 2026; 28(9):2110-2122.
ID #141 The Use of MEK Inhibitors for Neurofibromatosis Type 1-Associated High Grade Glioma and High-Grade Astrocytoma with Piloid Features in Children and Young Adults: A Real-World Cohort Analysis. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.032.
MEK inhibitors for neurofibromatosis type 1-associated central and peripheral nervous system tumors. Neuro-Oncology Advances. 2026; 8(Suppl 2):ii14-ii24.
Clinical safety and efficacy of bevacizumab in combination with mitogen-activated protein kinase kinase inhibitor therapy for glioma: a retrospective analysis. Neuro-Oncology Pediatrics. 2026; 2(1).
The Prostate is a Common Site of Disease in Patients with MEN2B and Medullary Thyroid Carcinoma. Endocrine-Related Cancer. 2026; 33(1).
ID #1015 A murine model system for IDH-mutant 1p/19q-codeleted oligodendroglioma. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.446.
Murine modeling of IDH-mutant 1p/19q-codeleted oligodendroglioma reveals genotype specific phenotypes. Neuro-Oncology. 2026.
ID #1132 CONNECT TarGeT-A molecularly-guided phase 2 trial for children and young adults newly diagnosed with high-grade glioma (HGG), including diffuse intrinsic pontine glioma (DIPG): (1) Ribociclib and everolimus for HGG/DIPG with cell cycle and/or PI3K/mTOR pathway alterations, and (2) Ribociclib and temozolomide for diffuse hemispheric glioma (DHG), H3G34-mutant. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.514.
ID #1122 Preliminary feasibility of an international, multidisciplinary central screening platform for the CONNECT TarGeT molecularly-guided phase 2 umbrella trial for children and young adults with newly-diagnosed high-grade glioma (HGG) including diffuse intrinsic pontine glioma (DIPG) Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.507.
Integrated clinical and molecular landscape of disseminated pediatric low-grade glioma. Neuro-Oncology. 2026; 28(2):535-551.
Maternal-Fetal Transmission of Diffuse Large B-Cell Lymphoma. Pediatric Blood and Cancer. 2026; 73(2):e32174.
Optimizing Haploidentical Donor Selection for Pediatric Hematopoietic Cell Transplant. Journal of Clinical Oncology. 2026; 44(11):1003-1015.
Peripheral blasts at apheresis as a risk factor for survival after tisagenlecleucel in children and young adults. Blood advances. 2026; 10(20):7115-7124.
A multi-institutional report of children with atypical teratoid rhabdoid tumor treated with intensive multimodal therapy. Neuro-Oncology Practice. 2026; 13(4):807-815.
Heart transplantation in pediatric oncology patients. JHLT Open. 2026; 12:100514.
Duration of Cryopreservation of Third-party Viral Specific T-cells (TP-VSTs) Does Not Influence Clinical Efficacy. Transplantation and Cellular Therapy. 2026.
Duration of Cryopreservation of Third-Party Viral Specific T-Cells (TP-VSTs) Does Not Influence Clinical Efficacy. Transplantation and Cellular Therapy. 2026; 32(2):s131.
Multi-institutional analysis of pediatric relapsed/progressive central nervous system germinomas. Clinical Oncology. 2026; 57:104266.
Feasibility Trial of a Tailored Adherence-Promotion Intervention for Adolescents and Young Adults With Cancer. Pediatric Blood and Cancer. 2026; 73(1):e32127.
HLH-like syndromes associate with increased risk of death and CD19- relapse after CAR T in pediatric B-ALL. Blood advances. 2026; 10(19):6422-6434.
Validation of a Pre-Infusion Prediction Model for IEC-HS in Children and Young Adults with B-Acute Lymphoblastic Leukemia. Transplantation and Cellular Therapy. 2026; 32(2):s580.
New Approaches to Clinical Trials for Rare Diseases: Decentralized Trial Design for Neurofibromatosis Type 1 and Schwannomatosis. Cancers. 2026; 18(15).
ID #890 Multi-institutional analysis of outcomes of pediatric patients with high-risk (HR) WNT-subtype medulloblastoma. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.384.
ID #634 Case Series of the Use of Trihexyphenidyl for Tremors in Pediatric Brain Tumors. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.247.
ID #472 Burnout Among Advanced Practice Providers in a Pediatric Oncology Setting. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.168.
ID #1002 Hematologic Toxicity during Proton Radiation: a Review of Weekly CBC Results at a Single Center. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.440.
Small Patients, Big Questions: Contemporary Therapeutic Strategies in Infants With Newly Diagnosed B-Cell Acute Lymphoblastic Leukemia. The Hematologist. 2026; 23(4).
Diagnostic pitfall: BCOR immunoreactivity in a molecularly confirmed astroblastoma, MN1-altered (HGNET-MN1). Clinical Neuropathology. 2026; 45(1):32-35.
Group 4 Medulloblastomas of Early Childhood Treated With High-Dose Chemotherapy- and Craniospinal Irradiation-Sparing Approach. Pediatric Blood and Cancer. 2026; 73(5):e70181.
All hands on DEK: structural insights into a unique histone modifier and chromatin remodeler. Epigenetics and Chromatin. 2026; 19(1).
One Size Doesn’t Fit All: International Consensus Recommendations for Pediatric Acute Myeloid Leukemia. The Hematologist. 2026; 23(5).
First, Do No Transplant? Emerging Evidence for Watchful Waiting in Select Juvenile Myelomonocytic Leukemia Patients. The Hematologist. 2026; 23(2).
No Data Zone Hope on Hold: Novel Drug Access Out of Reach for Children With Acute Myeloid Leukemia Despite Adult Successes. The Hematologist. 2026; 23(1).
Impact of Extramedullary Disease at Diagnosis on Outcomes Post Allogeneic Hematopoietic Cell Transplant in Children and Young Adults With Acute Myeloid Leukemia: A CIBMTR Report. Transplantation and Cellular Therapy. 2026; 32(5):580.e1-580.e18.
An analysis of PD1 pathway activity in malignant pediatric central nervous system tumors: a pediatric brain tumor consortium study, PBTC-N13. Neuro-Oncology Pediatrics. 2026; 2(2):wuag020.
028 Prevalence of optic nerve hypoplasia in neurofibromatosis type 1. Journal of AAPOS. 2026; 30(4):104940.
ID #476 Increased Prevalence of Optic Nerve Hypoplasia in Neurofibromatosis Type 1. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.170.
ID #18 CHD7-associated CHARGE Syndrome and a spinal schwannoma with a SH3PXD2A::HTRA1 fusion: A case report. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.001.
The first described report of a patient with CHD7-associated CHARGE syndrome and a spinal schwannoma with a SH3PXD2A::HTRA1 fusion; a case report and review of literature. Neuro-Oncology Pediatrics. 2026; 2(2):wuag034.
Overview of the neurotrophic tyrosine receptor kinase signaling pathway and therapeutic applications to brain tumors. In: Handbook of Brain Tumor Chemotherapy Molecular Therapeutics and Immunotherapy. 2026:501-513.
Chapter 29 Overview of the neurotrophic tyrosine receptor kinase signaling pathway and therapeutic applications to brain tumors. In: Handbook of Brain Tumor Chemotherapy, Molecular Therapeutics, and Immunotherapy. Elsevier; 2026:501-513.
ID #1028 A Retrospective Review Characterizing the Toxicities, Outcomes, and Molecular Characteristics of Adolescent and Young Adult Patients with Medulloblastoma. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.457.
Associations of Patient Age, Tumor Nephrectomy Weight, and Tumor Diameter With Event-free and Overall Survival in Stage I or II Favorable Histology Wilms Tumor: A Pooled Analysis of Children's Oncology Group Studies AREN0532 and AREN03B2. Annals of Surgery. 2026; 284(4):759-767.
Retrospective Case Series Highlighting the Real-World Experience of Nirogacestat Therapy in Young Adults With Desmoid Tumors. Pediatric Blood and Cancer. 2026; 73(9):e70517.
ENCERT: A Multisite Phase 1 Trial Using Everolimus in Combination With Nelarabine, Cyclophosphamide, and Etoposide in Relapsed T-Cell Lymphoblastic Leukemia/Lymphoma. Pediatric Blood and Cancer. 2026; 73(11):e70662.
Abstract 2548: Circulating proteomic signatures for subtyping NF1 associated peripheral nerve sheath tumors. Cancer Research. 2026; 86(7_Supplement):2548-2548.
ID #854 Updated findings from a phase 1 study of savolitinib in recurrent, progressive, or refractory medulloblastoma (MB), high-grade glioma (HGG), diffuse intrinsic pontine glioma (DIPG), and central nervous system (CNS) tumors harboring MET aberrations: A Pediatric Brain Tumor Consortium Trial: PBTC-049. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.360.
ID #651 A phase 1/2 and surgical Pediatric Brain Tumor Consortium (PBTC) study evaluating the casein kinase 2 (CK2) inhibitor CX-4945 (silmitasertib sodium) in children and adults with recurrent sonic hedgehog (SHH) medulloblastoma (MB): PBTC-053. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.260.
Risk of developing malignant peripheral nerve sheath tumors in patients with neurofibromatosis 1 receiving MEK inhibitor treatment for plexiform neurofibromas. Neuro-Oncology Advances. 2026; 8(1):vdag201.
The potential and risks of FLASH radiotherapy in pediatric patients. Neuro-Oncology Pediatrics. 2026; 2(1):wuaf014.
Parallels in Canonical Developmental Signaling Pathways between Normal Development and the Tumor Microenvironment. Cold Spring Harbor Perspectives in Medicine. 2026; 16(7).
Phase II One Arm Multicenter Study of Early Reinfusion of Tisagenlecleucel to Promote Durable B-cell Aplasia in Pediatric and Young Adult Patients with relapsed/refractory CD19-Positive B-cell Acute Lymphoblastic Leukemia (REFUEL) Transplantation and Cellular Therapy. 2026; 32(2):s593-s594.
Long-Term Hematologic Effects of Selumetinib Treatment in Children With Neurofibromatosis Type 1-Associated Plexiform Neurofibromas. Pediatric Blood and Cancer. 2026; 73(9):e70477.
ID #761 Feasibility study of hypofractionated radiotherapy in the setting of recurrent diffuse intrinsic pontine glioma. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.320.
Re-irradiation practices and outcomes in patients with diffuse intrinsic pontine glioma (DIPG): A report from the International DIPG/DMG Registry. Neuro-Oncology Pediatrics. 2026; 2(2):wuag013.
Lipid reprogramming of stratified squamous epithelium by the high-risk HPV E6 and E6/E7 oncoproteins. Metabolomics. 2026; 22(4).
ID #130 First Report of SHH-Activated Medulloblastoma in a Child With RRAS2-Related Noonan Syndrome. Neuro-Oncology Pediatrics. 2026; 2(Supplement_1):wuag026.025.
Scaffolding-dependent CASP1 constrains excessive cell-intrinsic inflammatory signaling in leukemia. Cell Chemical Biology. 2026; 33(1):59-73.e10.
A frontal lobe mass in a 6-year-old girl. Brain Pathology. 2026; e70132.
Evolution of Peripheral Nerve Sheath Tumors in Neurofibromatosis Type 1: Opportunities for Prevention and Therapeutic Strategies. Annual Review of Cancer Biology. 2026; 10(1):223-241.
Cumulative dose of chemotherapy and survival outcomes in children with average-risk medulloblastoma treated on Children's Oncology Group study ACNS0331. Neuro-Oncology. 2026; 28(7):1772-1780.
Abstract IA04: Identifying and targeting tumorigenic signals in the developing liver. Cancer Research. 2026; 86(18_Supplement_1):ia04-ia04.
Real-world experience with IDH inhibitors in pediatric patients with IDH1- and IDH2-mutated acute myeloid leukemia and myelodysplastic syndrome. Haematologica. 2026.
A Framework for Prioritizing Novel Agents in Malignant Peripheral Nerve Sheath Tumor Trials: A report from the Neurofibromatosis Clinical Trials Consortium. Neuro-Oncology. 2026.