Differential CXCR4 expression on hematopoietic progenitor cells versus stem cells directs homing and engraftment.
Felker, S; Shrestha, A; Bailey, J; Pillis, DM; Siniard, D; Malik, P.
JCI insight.
2022;
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NRASQ61R mutation in human endothelial cells causes vascular malformations.
Boscolo, E; Pastura, P; Schrenk, S; Goines, J; Kang, R; Pillis, D; Malik, P; Le Cras, TD.
Angiogenesis.
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Successful use of veno-venous extracorporeal membrane oxygenation for acute chest syndrome in a child with sickle cell disease and SARS-CoV-2.
Koh, W; Malik, P; Whitehead, J; Morales, DL S; Hayes, D.
Pediatric Pulmonology.
2022;
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Safety and Efficacy of Aru-1801 in Patients with Sickle Cell Disease: Early Results from the Phase 1/2 Momentum Study of a Modified Gamma Globin Gene Therapy and Reduced Intensity Conditioning.
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Blood.
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Towards access for all: 1st Working Group Report for the Global Gene Therapy Initiative (GGTI).
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Gene Therapy.
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Rapid and automated quantitation of dense red blood cells: A robust biomarker of hydroxyurea treatment response.
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Blood Cells, Molecules, and Diseases.
2021;
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Early initiation of hydroxyurea (hydroxycarbamide) using individualised, pharmacokinetics-guided dosing can produce sustained and nearly pancellular expression of fetal haemoglobin in children with sickle cell anaemia.
Quinn, CT; Niss, O; Dong, M; Pfeiffer, A; Korpik, J; Reynaud, M; Bonar, H; Kalfa, TA; Smart, LR; Malik, P; et al.
British Journal of Haematology.
2021;
194:617-625.
Cardiac pathophysiology in sickle cell disease.
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Journal of Thrombosis and Thrombolysis.
2021;
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Implementation of near-universal hydroxyurea uptake among children with sickle cell anemia: A single-center experience.
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Pediatric Blood and Cancer.
2021;
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FT-4202, an oral PKR activator, has potent antisickling effects and improves RBC survival and Hb levels in SCA mice.
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Blood Advances.
2021;
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